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Mavoglurant in Fragile X Syndrome: Results of two open-label, extension trials in adults and adolescents.
Hagerman, Randi; Jacquemont, Sebastien; Berry-Kravis, Elizabeth; Des Portes, Vincent; Stanfield, Andrew; Koumaras, Barbara; Rosenkranz, Gerd; Murgia, Alessandra; Wolf, Christian; Apostol, George; von Raison, Florian.
Afiliación
  • Hagerman R; MIND Institute and Department of Pediatrics, UC Davis Medical Center, Sacramento, CA, USA.
  • Jacquemont S; Centre Hospitalier Universitaire Vaudois, Lausanne, Switzerland.
  • Berry-Kravis E; CHU Sainte-Justine Research Centre, Montreal, Canada.
  • Des Portes V; Rush University Medical Centre, Department of Pediatrics, Neurological Sciences, and Biochemistry, Chicago, IL, USA.
  • Stanfield A; National Reference Center for Fragile X and Other XLID, CIC 1407 INSERM - Hospices Civils de Lyon, Université de Lyon and CNRS UMR 5304 (L2C2), Bron, France.
  • Koumaras B; Patrick Wild Centre, Division of Psychiatry, University of Edinburgh, Royal Edinburgh Hospital, Edinburgh, UK.
  • Rosenkranz G; Neurodegeneration Global Development, Novartis Pharmaceuticals Corporation, East Hanover, NJ, USA.
  • Murgia A; Neuroscience Development, Novartis Pharma AG, Basel, Switzerland.
  • Wolf C; Laboratory of Molecular Genetics of Neurodevelopment, Department of Women's and Children's Health, University of Padova, Padova, Italy.
  • Apostol G; Lycalis sprl, Brussels, Belgium.
  • von Raison F; Neuroscience Development, Novartis Pharma AG, Basel, Switzerland.
Sci Rep ; 8(1): 16970, 2018 11 19.
Article en En | MEDLINE | ID: mdl-30451888

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Antagonistas de Aminoácidos Excitadores / Síndrome del Cromosoma X Frágil / Indoles Tipo de estudio: Clinical_trials / Diagnostic_studies Límite: Adolescent / Adult / Child / Female / Humans / Male / Middle aged Idioma: En Revista: Sci Rep Año: 2018 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Reino Unido

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Antagonistas de Aminoácidos Excitadores / Síndrome del Cromosoma X Frágil / Indoles Tipo de estudio: Clinical_trials / Diagnostic_studies Límite: Adolescent / Adult / Child / Female / Humans / Male / Middle aged Idioma: En Revista: Sci Rep Año: 2018 Tipo del documento: Article País de afiliación: Estados Unidos Pais de publicación: Reino Unido