Detalhe da pesquisa
1.
Mitapivat versus Placebo for Pyruvate Kinase Deficiency.
N Engl J Med;
386(15): 1432-1442, 2022 04 14.
Artigo
em Inglês
| MEDLINE
| ID: mdl-35417638
2.
An update on pediatric ITP: differentiating primary ITP, IPD, and PID.
Blood;
140(6): 542-555, 2022 08 11.
Artigo
em Inglês
| MEDLINE
| ID: mdl-34479363
3.
Clinically meaningful improvements in patient-reported outcomes in mitapivat-treated patients with pyruvate kinase deficiency.
Am J Hematol;
2024 May 07.
Artigo
em Inglês
| MEDLINE
| ID: mdl-38712615
4.
HLA antibodies in fetal and neonatal alloimmune thrombocytopenia.
Transfusion;
63(6): 1141-1149, 2023 06.
Artigo
em Inglês
| MEDLINE
| ID: mdl-37038316
5.
Utilization of an ITP quality improvement pathway improves adherence to management guidelines.
Pediatr Blood Cancer;
70(3): e30074, 2023 03.
Artigo
em Inglês
| MEDLINE
| ID: mdl-36518083
6.
Pediatric refractory immune thrombocytopenia: A systematic review.
Pediatr Blood Cancer;
70(3): e30173, 2023 03.
Artigo
em Inglês
| MEDLINE
| ID: mdl-36579787
7.
Safety and Efficacy of Mitapivat in Pyruvate Kinase Deficiency.
N Engl J Med;
381(10): 933-944, 2019 09 05.
Artigo
em Inglês
| MEDLINE
| ID: mdl-31483964
8.
Management of pyruvate kinase deficiency in children and adults.
Blood;
136(11): 1241-1249, 2020 09 10.
Artigo
em Inglês
| MEDLINE
| ID: mdl-32702739
9.
Thrombopoietin receptor agonists and rituximab for treatment of pediatric immune thrombocytopenia: A systematic review and meta-analysis of prospective clinical trials.
Pediatr Blood Cancer;
69(3): e29447, 2022 03.
Artigo
em Inglês
| MEDLINE
| ID: mdl-34962697
10.
Diagnosis, monitoring, and management of pyruvate kinase deficiency in children.
Pediatr Blood Cancer;
69(8): e29696, 2022 08.
Artigo
em Inglês
| MEDLINE
| ID: mdl-35452178
11.
Characteristics and outcomes of autoimmune hemolytic anemia after pediatric allogeneic stem cell transplant.
Pediatr Blood Cancer;
69(1): e29410, 2022 01.
Artigo
em Inglês
| MEDLINE
| ID: mdl-34709706
12.
The pyruvate kinase (PK) to hexokinase enzyme activity ratio and erythrocyte PK protein level in the diagnosis and phenotype of PK deficiency.
Br J Haematol;
192(6): 1092-1096, 2021 03.
Artigo
em Inglês
| MEDLINE
| ID: mdl-32463523
13.
Refractory autoimmune cytopenias in pediatric Evans syndrome with underlying systemic immune dysregulation.
Eur J Haematol;
106(6): 783-787, 2021 Jun.
Artigo
em Inglês
| MEDLINE
| ID: mdl-33570766
14.
Comorbidities and complications in adults with pyruvate kinase deficiency.
Eur J Haematol;
106(4): 484-492, 2021 Apr.
Artigo
em Inglês
| MEDLINE
| ID: mdl-33370479
15.
Quality of life is an important indication for second-line treatment in children with immune thrombocytopenia.
Pediatr Blood Cancer;
68(6): e29023, 2021 06.
Artigo
em Inglês
| MEDLINE
| ID: mdl-33764667
16.
Pyruvate kinase deficiency in children.
Pediatr Blood Cancer;
68(9): e29148, 2021 09.
Artigo
em Inglês
| MEDLINE
| ID: mdl-34125488
17.
Immune dysregulation and multisystem inflammatory syndrome in children (MIS-C) in individuals with haploinsufficiency of SOCS1.
J Allergy Clin Immunol;
146(5): 1194-1200.e1, 2020 11.
Artigo
em Inglês
| MEDLINE
| ID: mdl-32853638
18.
Fatigue in children and adolescents with immune thrombocytopenia.
Br J Haematol;
191(1): 98-106, 2020 10.
Artigo
em Inglês
| MEDLINE
| ID: mdl-32501532
19.
Clinical spectrum of pyruvate kinase deficiency: data from the Pyruvate Kinase Deficiency Natural History Study.
Blood;
131(20): 2183-2192, 2018 05 17.
Artigo
em Inglês
| MEDLINE
| ID: mdl-29549173
20.
The variable manifestations of disease in pyruvate kinase deficiency and their management.
Haematologica;
105(9): 2229-2239, 2020 09 01.
Artigo
em Inglês
| MEDLINE
| ID: mdl-33054048