Detalhe da pesquisa
1.
Phenotypic Characterization and Comparison of Cystic Fibrosis Rat Models Generated Using CRISPR/Cas9 Gene Editing.
Am J Pathol;
190(5): 977-993, 2020 05.
Artigo
em Inglês
| MEDLINE
| ID: mdl-32084371
2.
Correction of murine mucopolysaccharidosis type IIIA central nervous system pathology by intracerebroventricular lentiviral-mediated gene delivery.
J Gene Med;
16(11-12): 374-87, 2014.
Artigo
em Inglês
| MEDLINE
| ID: mdl-25418946
3.
Transduction of ferret airway epithelia using a pre-treatment and lentiviral gene vector.
BMC Pulm Med;
14: 183, 2014 Nov 21.
Artigo
em Inglês
| MEDLINE
| ID: mdl-25413892
4.
Neurocognitive testing in a murine model of mucopolysaccharidosis type IIIA.
Mol Genet Metab Rep;
36: 100985, 2023 Sep.
Artigo
em Inglês
| MEDLINE
| ID: mdl-37332488
5.
Skeletal response to lentiviral mediated gene therapy in a mouse model of MPS VII.
Mol Genet Metab;
106(2): 202-13, 2012 Jun.
Artigo
em Inglês
| MEDLINE
| ID: mdl-22525091
6.
Systemic scAAV9.U1a.hSGSH Delivery Corrects Brain Biochemistry in Mucopolysaccharidosis Type IIIA at Early and Later Stages of Disease.
Hum Gene Ther;
32(7-8): 420-430, 2021 04.
Artigo
em Inglês
| MEDLINE
| ID: mdl-33339477
7.
Correction of mucopolysaccharidosis type IIIA somatic and central nervous system pathology by lentiviral-mediated gene transfer.
J Gene Med;
12(9): 717-28, 2010 Sep.
Artigo
em Inglês
| MEDLINE
| ID: mdl-20683858
8.
Comparison of ventricular and intravenous lentiviral-mediated gene therapy for murine MPS VII.
Mol Genet Metab;
101(4): 370-82, 2010 Dec.
Artigo
em Inglês
| MEDLINE
| ID: mdl-20864369
9.
Collection of cerebrospinal fluid from murine lateral ventricles for biomarker determination in mucopolysaccharidosis type IIIA.
J Neurosci Methods;
324: 108314, 2019 08 01.
Artigo
em Inglês
| MEDLINE
| ID: mdl-31202732
10.
Transient Lentiviral Vector Production Using a Packed-Bed Bioreactor System.
Hum Gene Ther Methods;
30(3): 93-101, 2019 06.
Artigo
em Inglês
| MEDLINE
| ID: mdl-31084376
11.
Lentiviral-mediated gene therapy for murine mucopolysaccharidosis type IIIA.
Mol Genet Metab;
93(4): 411-8, 2008 Apr.
Artigo
em Inglês
| MEDLINE
| ID: mdl-18248829
12.
Lobe-Specific Gene Vector Delivery to Rat Lungs Using a Miniature Bronchoscope.
Hum Gene Ther Methods;
29(5): 228-235, 2018 10.
Artigo
em Inglês
| MEDLINE
| ID: mdl-29993287
13.
Large-scale production of lentiviral vectors using multilayer cell factories.
J Biol Methods;
5(2): e90, 2018.
Artigo
em Inglês
| MEDLINE
| ID: mdl-31453241
14.
Role of Basal Cells in Producing Persistent Lentivirus-Mediated Airway Gene Expression.
Hum Gene Ther;
29(6): 653-662, 2018 06.
Artigo
em Inglês
| MEDLINE
| ID: mdl-29179571
15.
Lentiviral-mediated gene correction of mucopolysaccharidosis type IIIA.
Genet Vaccines Ther;
5: 1, 2007 Jan 16.
Artigo
em Inglês
| MEDLINE
| ID: mdl-17227588
16.
Challenges of up-scaling lentivirus production and processing.
J Biotechnol;
240: 23-30, 2016 Dec 20.
Artigo
em Inglês
| MEDLINE
| ID: mdl-27769802
17.
Correction of methylmalonic aciduria in vivo using a codon-optimized lentiviral vector.
Hum Gene Ther;
25(6): 529-38, 2014 Jun.
Artigo
em Inglês
| MEDLINE
| ID: mdl-24568291
18.
Therapies for neurological disease in the mucopolysaccharidoses.
Curr Gene Ther;
11(2): 132-43, 2011 Apr.
Artigo
em Inglês
| MEDLINE
| ID: mdl-21291356