Detalhe da pesquisa
1.
Innovations in RNA therapy for hemophilia.
Blood;
142(19): 1613-1621, 2023 11 09.
Artigo
em Inglês
| MEDLINE
| ID: mdl-37478403
2.
Multiyear Factor VIII Expression after AAV Gene Transfer for Hemophilia A.
N Engl J Med;
385(21): 1961-1973, 2021 11 18.
Artigo
em Inglês
| MEDLINE
| ID: mdl-34788507
3.
Observational cohort study of long-term outcomes of liver transplantation in haemophilia.
Haemophilia;
30(1): 87-97, 2024 Jan.
Artigo
em Inglês
| MEDLINE
| ID: mdl-38111071
4.
BIVV001 Fusion Protein as Factor VIII Replacement Therapy for Hemophilia A.
N Engl J Med;
383(11): 1018-1027, 2020 09 10.
Artigo
em Inglês
| MEDLINE
| ID: mdl-32905674
5.
Prevalence and risk factors for hepatocellular carcinoma in individuals with haemophilia in the era of direct-acting antiviral agents: A national inpatient sample study.
Haemophilia;
28(5): 769-775, 2022 Sep.
Artigo
em Inglês
| MEDLINE
| ID: mdl-35727998
6.
Quality of life in a large multinational haemophilia B cohort (The B-Natural study) - Unmet needs remain.
Haemophilia;
28(3): 453-461, 2022 May.
Artigo
em Inglês
| MEDLINE
| ID: mdl-35263495
7.
Factor VIII concentrate dosing with lean body mass, ideal body weight and total body weight in overweight and obesity: A randomized, controlled, open-label, 3 × 3 crossover trial.
Haemophilia;
27(3): 351-357, 2021 May.
Artigo
em Inglês
| MEDLINE
| ID: mdl-33749970
8.
Quality of periprocedural care in patients with von Willebrand disease.
Haemophilia;
27(5): 830-836, 2021 Sep.
Artigo
em Inglês
| MEDLINE
| ID: mdl-34343372
9.
Natural history study of factor IX deficiency with focus on treatment and complications (B-Natural).
Haemophilia;
27(1): 49-59, 2021 Jan.
Artigo
em Inglês
| MEDLINE
| ID: mdl-33278853
10.
Long-Term Follow-Up of the First in Human Intravascular Delivery of AAV for Gene Transfer: AAV2-hFIX16 for Severe Hemophilia B.
Mol Ther;
28(9): 2073-2082, 2020 09 02.
Artigo
em Inglês
| MEDLINE
| ID: mdl-32559433
11.
Targeting of Antithrombin in Hemophilia A or B with RNAi Therapy.
N Engl J Med;
377(9): 819-828, 2017 08 31.
Artigo
em Inglês
| MEDLINE
| ID: mdl-28691885
12.
Hemophilia B Gene Therapy with a High-Specific-Activity Factor IX Variant.
N Engl J Med;
377(23): 2215-2227, 2017 12 07.
Artigo
em Inglês
| MEDLINE
| ID: mdl-29211678
13.
Traumatic injury results in prolonged circulation of ultralarge von Willebrand factor and a reduction in ADAMTS13 activity.
Transfusion;
60(6): 1308-1318, 2020 06.
Artigo
em Inglês
| MEDLINE
| ID: mdl-32441353
14.
Emicizumab prophylaxis in patients with haemophilia A with and without inhibitors.
Haemophilia;
26(1): 41-46, 2020 Jan.
Artigo
em Inglês
| MEDLINE
| ID: mdl-31746522
15.
The impact of extended half-life factor concentrates on prophylaxis for severe hemophilia in the United States.
Am J Hematol;
95(8): 960-965, 2020 08.
Artigo
em Inglês
| MEDLINE
| ID: mdl-32356313
16.
The national blueprint for future factor VIII inhibitor clinical trials: NHLBI State of the Science (SOS) Workshop on factor VIII inhibitors.
Haemophilia;
25(4): 581-589, 2019 Jul.
Artigo
em Inglês
| MEDLINE
| ID: mdl-31329364
17.
Incidence and risk factors for hepatocellular cancer in individuals with haemophilia: A National Inpatient Sample Study.
Haemophilia;
25(2): 221-228, 2019 Mar.
Artigo
em Inglês
| MEDLINE
| ID: mdl-30615816
18.
Platelet VIII pack evades immune detection.
Blood;
127(10): 1222-4, 2016 Mar 10.
Artigo
em Inglês
| MEDLINE
| ID: mdl-26965921
19.
Clinical and laboratory variability in a cohort of patients diagnosed with type 1 VWD in the United States.
Blood;
127(20): 2481-8, 2016 05 19.
Artigo
em Inglês
| MEDLINE
| ID: mdl-26862110
20.
Prophylactic rtPA in the Prevention of Line-associated Thrombosis and Infection in Short Bowel Syndrome.
J Pediatr Gastroenterol Nutr;
66(6): 972-975, 2018 Jun.
Artigo
em Inglês
| MEDLINE
| ID: mdl-29135819