Detalhe da pesquisa
1.
Ablation of SYK Kinase from Expanded Primary Human NK Cells via CRISPR/Cas9 Enhances Cytotoxicity and Cytokine Production.
J Immunol;
210(8): 1108-1122, 2023 04 15.
Artigo
em Inglês
| MEDLINE
| ID: mdl-36881874
2.
Evolution of the clinical-stage hyperactive TcBuster transposase as a platform for robust non-viral production of adoptive cellular therapies.
Mol Ther;
32(6): 1817-1834, 2024 Jun 05.
Artigo
em Inglês
| MEDLINE
| ID: mdl-38627969
3.
Generation and characterization of an immunodeficient mouse model of mucopolysaccharidosis type II.
Mol Genet Metab;
138(4): 107539, 2023 04.
Artigo
em Inglês
| MEDLINE
| ID: mdl-37023503
4.
CRISPR-Cas9 base editors and their current role in human therapeutics.
Cytotherapy;
25(3): 270-276, 2023 03.
Artigo
em Inglês
| MEDLINE
| ID: mdl-36635153
5.
Correction of Fanconi Anemia Mutations Using Digital Genome Engineering.
Int J Mol Sci;
23(15)2022 Jul 29.
Artigo
em Inglês
| MEDLINE
| ID: mdl-35955545
6.
A Pan-RNase Inhibitor Enabling CRISPR-mRNA Platforms for Engineering of Primary Human Monocytes.
Int J Mol Sci;
23(17)2022 Aug 28.
Artigo
em Inglês
| MEDLINE
| ID: mdl-36077152
7.
Comparative international incidence of Ewing sarcoma 1988 to 2012.
Int J Cancer;
149(5): 1054-1066, 2021 09 01.
Artigo
em Inglês
| MEDLINE
| ID: mdl-33961701
8.
A Genetically Engineered Primary Human Natural Killer Cell Platform for Cancer Immunotherapy.
Mol Ther;
28(1): 52-63, 2020 01 08.
Artigo
em Inglês
| MEDLINE
| ID: mdl-31704085
9.
Advancing gene targeting for primary immune deficiencies: Adenine base editing of the human IL2RG locus for correction of SCID-X1.
Mol Ther;
32(6): 1606-1608, 2024 Jun 05.
Artigo
em Inglês
| MEDLINE
| ID: mdl-38781958
10.
Aryl hydrocarbon receptor inhibition promotes hematolymphoid development from human pluripotent stem cells.
Blood;
129(26): 3428-3439, 2017 06 29.
Artigo
em Inglês
| MEDLINE
| ID: mdl-28533309
11.
CRISPR/Cas9-Based Cellular Engineering for Targeted Gene Overexpression.
Int J Mol Sci;
19(4)2018 Mar 22.
Artigo
em Inglês
| MEDLINE
| ID: mdl-29565806
12.
Rapid generation of Col7a1-/- mouse model of recessive dystrophic epidermolysis bullosa and partial rescue via immunosuppressive dermal mesenchymal stem cells.
Lab Invest;
97(10): 1218-1224, 2017 10.
Artigo
em Inglês
| MEDLINE
| ID: mdl-28892093
13.
Angiotensin receptor blockade mediated amelioration of mucopolysaccharidosis type I cardiac and craniofacial pathology.
J Inherit Metab Dis;
40(2): 281-289, 2017 03.
Artigo
em Inglês
| MEDLINE
| ID: mdl-27743312
14.
Evaluation of TCR Gene Editing Achieved by TALENs, CRISPR/Cas9, and megaTAL Nucleases.
Mol Ther;
24(3): 570-81, 2016 Mar.
Artigo
em Inglês
| MEDLINE
| ID: mdl-26502778
15.
CRISPR/Cas9-Mediated Correction of the FANCD1 Gene in Primary Patient Cells.
Int J Mol Sci;
18(6)2017 Jun 14.
Artigo
em Inglês
| MEDLINE
| ID: mdl-28613254
16.
In Vitro T-Cell Generation From Adult, Embryonic, and Induced Pluripotent Stem Cells: Many Roads to One Destination.
Stem Cells;
33(11): 3174-80, 2015 Nov.
Artigo
em Inglês
| MEDLINE
| ID: mdl-26227158
17.
From marrow to matrix: novel gene and cell therapies for epidermolysis bullosa.
Mol Ther;
23(6): 987-992, 2015 Jun.
Artigo
em Inglês
| MEDLINE
| ID: mdl-25803200
18.
Trp53 haploinsufficiency modifies EGFR-driven peripheral nerve sheath tumorigenesis.
Am J Pathol;
184(7): 2082-98, 2014 Jul.
Artigo
em Inglês
| MEDLINE
| ID: mdl-24832557
19.
DNA methylation of Runx1 regulatory regions correlates with transition from primitive to definitive hematopoietic potential in vitro and in vivo.
Blood;
122(17): 2978-86, 2013 Oct 24.
Artigo
em Inglês
| MEDLINE
| ID: mdl-24030384
20.
TALEN-based gene correction for epidermolysis bullosa.
Mol Ther;
21(6): 1151-9, 2013 Jun.
Artigo
em Inglês
| MEDLINE
| ID: mdl-23546300