Your browser doesn't support javascript.
loading
Impact of elosulfase alfa in patients with morquio A syndrome who have limited ambulation: An open-label, phase 2 study.
Harmatz, Paul R; Mengel, Eugen; Geberhiwot, Tarekegn; Muschol, Nicole; Hendriksz, Christian J; Burton, Barbara K; Jameson, Elisabeth; Berger, Kenneth I; Jester, Andrea; Treadwell, Marsha; Sisic, Zlatko; Decker, Celeste.
Afiliação
  • Harmatz PR; UCSF Benioff Children's Hospital Oakland, Oakland, California.
  • Mengel E; Mainz University Medical Center, Mainz, Germany.
  • Geberhiwot T; New Queen Elizabeth Hospital, Birmingham, UK.
  • Muschol N; University Hospital Hamburg-Eppendorf, Hamburg, Germany.
  • Hendriksz CJ; Salford Royal Foundation NHS Trust, Salford, UK.
  • Burton BK; Ann & Robert H. Lurie Children's Hospital and Northwestern University Feinberg School of Medicine, Chicago, Illinois.
  • Jameson E; Willink Unit, Manchester Centre for Genomic Medicine, Manchester Academic Health Sciences Centre, St Mary's Hospital, University of Manchester, CMFT, Manchester, UK.
  • Berger KI; NY University School of Medicine, New York, New York.
  • Jester A; Birmingham Children's Hospital, Birmingham, UK.
  • Treadwell M; UCSF Benioff Children's Hospital Oakland, Oakland, California.
  • Sisic Z; BioMarin Europe Ltd., London, UK.
  • Decker C; BioMarin Pharmaceutical Inc., Novato, California.
Am J Med Genet A ; 173(2): 375-383, 2017 Feb.
Article em En | MEDLINE | ID: mdl-27774754
Assuntos
Palavras-chave
Texto completo
Imprimir
XML
PubMed Links
Buscar no Google

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Condroitina Sulfatases / Caminhada / Mucopolissacaridose IV / Terapia de Reposição de Enzimas Tipo de estudo: Clinical_trials / Guideline Limite: Adolescent / Adult / Child / Female / Humans / Male Idioma: En Revista: Am J Med Genet A Assunto da revista: GENETICA MEDICA Ano de publicação: 2017 Tipo de documento: Article
Texto completo
Imprimir
XML
PubMed Links
Buscar no Google

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Condroitina Sulfatases / Caminhada / Mucopolissacaridose IV / Terapia de Reposição de Enzimas Tipo de estudo: Clinical_trials / Guideline Limite: Adolescent / Adult / Child / Female / Humans / Male Idioma: En Revista: Am J Med Genet A Assunto da revista: GENETICA MEDICA Ano de publicação: 2017 Tipo de documento: Article