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Systemic Delivery of MicroRNA Using Recombinant Adeno-associated Virus Serotype 9 to Treat Neuromuscular Diseases in Rodents.
Pourshafie, Naemeh; Lee, Philip R; Chen, Ke-Lian; Harmison, George G; Bott, Laura C; Fischbeck, Kenneth H; Rinaldi, Carlo.
Afiliação
  • Pourshafie N; Neurogenetics Branch, National Institute of Neurological Disorders and Stroke, National Institutes of Health.
  • Lee PR; Section on Nervous System Development and Plasticity, The Eunice Kennedy Shriver National Institute of Child and Human Development, National Institutes of Health.
  • Chen KL; Neurogenetics Branch, National Institute of Neurological Disorders and Stroke, National Institutes of Health.
  • Harmison GG; Neurogenetics Branch, National Institute of Neurological Disorders and Stroke, National Institutes of Health.
  • Bott LC; Neurogenetics Branch, National Institute of Neurological Disorders and Stroke, National Institutes of Health; Department of Molecular Biosciences, Rice Institute for Biomedical Research, Northwestern University.
  • Fischbeck KH; Neurogenetics Branch, National Institute of Neurological Disorders and Stroke, National Institutes of Health.
  • Rinaldi C; Neurogenetics Branch, National Institute of Neurological Disorders and Stroke, National Institutes of Health; Department of Physiology, Anatomy and Genetics, University of Oxford; carlo.rinaldi@dpag.ox.ac.uk.
J Vis Exp ; (138)2018 08 10.
Article em En | MEDLINE | ID: mdl-30148479

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Terapia Genética / Regulação da Expressão Gênica / MicroRNAs / Doenças Neuromusculares Tipo de estudo: Risk_factors_studies Limite: Animals / Humans Idioma: En Revista: J Vis Exp Ano de publicação: 2018 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Terapia Genética / Regulação da Expressão Gênica / MicroRNAs / Doenças Neuromusculares Tipo de estudo: Risk_factors_studies Limite: Animals / Humans Idioma: En Revista: J Vis Exp Ano de publicação: 2018 Tipo de documento: Article