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Potential Risks to Stable Long-term Outcome of Allogeneic Hematopoietic Stem Cell Transplantation for Children With Cerebral X-linked Adrenoleukodystrophy.
Kühl, Jörn-Sven; Kupper, Jana; Baqué, Hermann; Ebell, Wolfram; Gärtner, Jutta; Korenke, Christoph; Spors, Birgit; Steffen, Ingo G; Strauss, Gabriele; Voigt, Sebastian; Weschke, Bernhard; Weddige, Almuth; Köhler, Wolfgang; Steinfeld, Robert.
Afiliação
  • Kühl JS; Department of Pediatric Hematology/Oncology/Hemostaseology, University Hospital Leipzig, Leipzig, Germany.
  • Kupper J; Department of Pediatric Oncology/Hematology/SCT, Charité Campus Virchow-Klinikum, Berlin, Germany.
  • Baqué H; Department of Pediatric Neurology, Charité Campus Virchow-Klinikum, Berlin, Germany.
  • Ebell W; Department of Pediatric Oncology/Hematology/SCT, Charité Campus Virchow-Klinikum, Berlin, Germany.
  • Gärtner J; Department of Pediatric Neurology, University Medical Center Göttingen, Göttingen, Germany.
  • Korenke C; Department of Pediatric Neurology, Klinikum Oldenburg, Oldenburg, Germany.
  • Spors B; Department of Pediatric Radiology, Charité Campus Virchow-Klinikum, Berlin, Germany.
  • Steffen IG; Department of Pediatric Oncology/Hematology/SCT, Charité Campus Virchow-Klinikum, Berlin, Germany.
  • Strauss G; Department of Pediatrics, Helios-Klinikum Berlin-Buch, Berlin, Germany.
  • Voigt S; Department of Pediatric Oncology/Hematology/SCT, Charité Campus Virchow-Klinikum, Berlin, Germany.
  • Weschke B; Department of Pediatric Neurology, Charité Campus Virchow-Klinikum, Berlin, Germany.
  • Weddige A; Department of Pediatric Neurology, University Medical Center Göttingen, Göttingen, Germany.
  • Köhler W; Department of Neurology, University Hospital Leipzig, Leipzig, Germany.
  • Steinfeld R; Department of Pediatric Neurology, University Medical Center Göttingen, Göttingen, Germany.
JAMA Netw Open ; 1(3): e180769, 2018 07 06.
Article em En | MEDLINE | ID: mdl-30646031

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Transplante de Células-Tronco Hematopoéticas / Adrenoleucodistrofia Tipo de estudo: Etiology_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Child / Child, preschool / Humans / Male Idioma: En Revista: JAMA Netw Open Ano de publicação: 2018 Tipo de documento: Article País de afiliação: Alemanha

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Transplante de Células-Tronco Hematopoéticas / Adrenoleucodistrofia Tipo de estudo: Etiology_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Child / Child, preschool / Humans / Male Idioma: En Revista: JAMA Netw Open Ano de publicação: 2018 Tipo de documento: Article País de afiliação: Alemanha