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AAV-Genome Population Sequencing of Vectors Packaging CRISPR Components Reveals Design-Influenced Heterogeneity.
Tran, Ngoc Tam; Heiner, Cheryl; Weber, Kristina; Weiand, Michael; Wilmot, Daniella; Xie, Jun; Wang, Dan; Brown, Alexander; Manokaran, Sangeetha; Su, Qin; Zapp, Maria L; Gao, Guangping; Tai, Phillip W L.
Afiliação
  • Tran NT; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA 01605, USA.
  • Heiner C; Department of Microbiology and Physiological Systems, University of Massachusetts Medical School, Worcester, MA, 01605, USA.
  • Weber K; Pacific Biosciences, Inc., Menlo Park, CA 94025, USA.
  • Weiand M; Pacific Biosciences, Inc., Menlo Park, CA 94025, USA.
  • Wilmot D; Pacific Biosciences, Inc., Menlo Park, CA 94025, USA.
  • Xie J; Program in Molecular Medicine and Center for AIDS Research, University of Massachusetts Medical School, Worcester, MA 01605, USA.
  • Wang D; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA 01605, USA.
  • Brown A; Department of Microbiology and Physiological Systems, University of Massachusetts Medical School, Worcester, MA, 01605, USA.
  • Manokaran S; Viral Vector Core, University of Massachusetts Medical School, Worcester, MA 01605, USA.
  • Su Q; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA 01605, USA.
  • Zapp ML; Department of Microbiology and Physiological Systems, University of Massachusetts Medical School, Worcester, MA, 01605, USA.
  • Gao G; Horae Gene Therapy Center, University of Massachusetts Medical School, Worcester, MA 01605, USA.
  • Tai PWL; Department of Microbiology and Physiological Systems, University of Massachusetts Medical School, Worcester, MA, 01605, USA.
Mol Ther Methods Clin Dev ; 18: 639-651, 2020 Sep 11.
Article em En | MEDLINE | ID: mdl-32775498

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Methods Clin Dev Ano de publicação: 2020 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Methods Clin Dev Ano de publicação: 2020 Tipo de documento: Article País de afiliação: Estados Unidos