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A randomized, double-blind trial of triheptanoin for drug-resistant epilepsy in glucose transporter 1 deficiency syndrome.
Striano, Pasquale; Auvin, Stéphane; Collins, Abigail; Horvath, Rita; Scheffer, Ingrid E; Tzadok, Michal; Miller, Ian; Kay Koenig, Mary; Lacy, Adrian; Davis, Ronald; Garcia-Cazorla, Angela; Saneto, Russell P; Brandabur, Melanie; Blair, Susan; Koutsoukos, Tony; De Vivo, Darryl.
Afiliação
  • Striano P; G. Gaslini Institute, Scientific Institute for Research and Health Care, Genoa, Italy.
  • Auvin S; Departments of Neurosciences, Rehabilitation, Ophthalmology, Genetics, and Maternal and Child Health, University of Genoa, Genoa, Italy.
  • Collins A; Robert Debré University Hospital and University of Paris, Paris, France.
  • Horvath R; University Institute of France, Paris, France.
  • Scheffer IE; Children's Hospital Colorado, Aurora, Colorado, USA.
  • Tzadok M; Department of Clinical Neurosciences, University of Cambridge, Cambridge, UK.
  • Miller I; Austin and Royal Children's Hospital, Florey and Murdoch Institutes, University of Melbourne, Melbourne, Victoria, Australia.
  • Kay Koenig M; Pediatric Neurology Units, Edmond and Lily Safra Children's Hospital, Sheba Medical Center, Tel HaShomer, Affiliated with the Sackler Faculty of Medicine, Tel Aviv University, Ramat Gan, Israel.
  • Lacy A; Miami Children's Research Institute, Miami, Florida, USA.
  • Davis R; University of Texas Health Science Center at Houston, Houston, Texas, USA.
  • Garcia-Cazorla A; Cook Children's Medical Center, Fort Worth, Texas, USA.
  • Saneto RP; Neurology and Epilepsy Research Center, Pediatric Neurology, Orlando, Florida, USA.
  • Brandabur M; Sant Joan de Déu Hospital, Barcelona, Spain.
  • Blair S; Department of Neurology, Division of Pediatric Neurology, University of Washington/Seattle Children's Hospital, Seattle, Washington, USA.
  • Koutsoukos T; Ultragenyx Pharmaceutical Inc, Novato, California, USA.
  • De Vivo D; Ultragenyx Pharmaceutical Inc, Novato, California, USA.
Epilepsia ; 63(7): 1748-1760, 2022 07.
Article em En | MEDLINE | ID: mdl-35441706

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Triglicerídeos / Epilepsia Tipo Ausência / Epilepsia Resistente a Medicamentos Tipo de estudo: Clinical_trials Limite: Adolescent / Adult / Child / Humans Idioma: En Revista: Epilepsia Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Itália

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Triglicerídeos / Epilepsia Tipo Ausência / Epilepsia Resistente a Medicamentos Tipo de estudo: Clinical_trials Limite: Adolescent / Adult / Child / Humans Idioma: En Revista: Epilepsia Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Itália