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Treatment of newly diagnosed severe aplastic anemia in children: Evidence-based recommendations.
Shimano, Kristin A; Rothman, Jennifer A; Allen, Steven W; Castillo, Paul; de Jong, Jill L O; Dror, Yigal; Geddis, Amy E; Lau, Bonnie W; McGuinn, Catherine; Narla, Anupama; Overholt, Kathleen; Pereda, Maria A; Sharathkumar, Anjali; Sasa, Ghadir; Nakano, Taizo A; Myers, Kasiani; Gloude, Nicholas J; Broglie, Larisa; Boklan, Jessica.
Afiliação
  • Shimano KA; Department of Pediatrics, Division of Allergy, Immunology, and Bone Marrow Transplant, University of California San Francisco Benioff Children's Hospital, San Francisco, California, USA.
  • Rothman JA; Department of Pediatrics, Division of Pediatric Hematology/Oncology, Duke University Medical Center, Durham, North Carolina, USA.
  • Allen SW; Department of Pediatrics, Pediatric Hematology/Oncology, University of Pittsburgh School of Medicine, UPMC Children's Hospital of Pittsburgh, Pittsburgh, Pennsylvania, USA.
  • Castillo P; Department of Pediatrics, Division of Pediatric Hematology Oncology, UF Health Shands Children's Hospital, Gainesville, Florida, USA.
  • de Jong JLO; Department of Pediatrics, Section of Hematology/Oncology/Stem Cell Transplantation, University of Chicago, Chicago, Illinois, USA.
  • Dror Y; Department of Pediatrics, Marrow Failure and Myelodysplasia Program, Division of Hematology/Oncology, The Hospital for Sick Children, Toronto, Canada.
  • Geddis AE; Department of Pediatrics, Cancer and Blood Disorders Center, Seattle Children's Hospital, Seattle, Washington, USA.
  • Lau BW; Department of Pediatrics, Pediatric Hematology-Oncology, Dartmouth-Hitchcock, Lebanon, New Hampshire, USA.
  • McGuinn C; Department of Pediatrics, Division of Pediatric Hematology Oncology, Weill Cornell Medicine, New York, New York, USA.
  • Narla A; Department of Pediatrics, Stanford University School of Medicine, Stanford, California, USA.
  • Overholt K; Department of Pediatrics, Pediatric Hematology/Oncology, Riley Hospital for Children at Indiana University, Indianapolis, Indiana, USA.
  • Pereda MA; Department of Pediatrics, Center for Cancer and Blood Disorders, Children's Hospital Colorado, Aurora, Colorado, USA.
  • Sharathkumar A; Stead Family Department of Pediatrics, University of Iowa Carver College of Medicine, Iowa City, Iowa, USA.
  • Sasa G; Sarah Cannon Transplant and Cellular Therapy Network, San Antonio, Texas, USA.
  • Nakano TA; Department of Pediatrics, Center for Cancer and Blood Disorders, Children's Hospital Colorado, Aurora, Colorado, USA.
  • Myers K; Department of Pediatrics, University of Cincinnati College of Medicine, Division of Bone Marrow Transplantation and Immune Deficiency, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, USA.
  • Gloude NJ; Department of Pediatrics, University of California San Diego, Rady Children's Hospital, San Diego, California, USA.
  • Broglie L; Department of Pediatric Hematology/Oncology/Blood and Marrow Transplantation, Medical College of Wisconsin, Milwaukee, Wisconsin, USA.
  • Boklan J; Department of Pediatrics, Center for Cancer and Blood Disorders, Phoenix Children's Hospital, Phoenix, Arizona, USA.
Pediatr Blood Cancer ; 71(8): e31070, 2024 Aug.
Article em En | MEDLINE | ID: mdl-38757488
ABSTRACT
Severe aplastic anemia (SAA) is a rare potentially fatal hematologic disorder. Although overall outcomes with treatment are excellent, there are variations in management approach, including differences in treatment between adult and pediatric patients. Certain aspects of treatment are under active investigation in clinical trials. Because of the rarity of the disease, some pediatric hematologists may have relatively limited experience with the complex management of SAA. The following recommendations reflect an up-to-date evidence-based approach to the treatment of children with newly diagnosed SAA.
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Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Anemia Aplástica Limite: Child / Humans Idioma: En Revista: Pediatr Blood Cancer Assunto da revista: HEMATOLOGIA / NEOPLASIAS / PEDIATRIA Ano de publicação: 2024 Tipo de documento: Article País de afiliação: Estados Unidos

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Anemia Aplástica Limite: Child / Humans Idioma: En Revista: Pediatr Blood Cancer Assunto da revista: HEMATOLOGIA / NEOPLASIAS / PEDIATRIA Ano de publicação: 2024 Tipo de documento: Article País de afiliação: Estados Unidos