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Voxelotor treatment of a patient with sickle cell disease and very severe anemia.
Shet, Arun S; Mendelsohn, Laurel; Harper, Julia; Ostrowski, David; Henry, Eric R; Gwaabe, Eveline; Nichols, Jim; Alayash, Abdu I; Eaton, William A; Thein, Swee Lay.
Afiliación
  • Shet AS; Sickle Cell Branch, National Heart Lung and Blood Institute, National Institutes of Health, Bethesda, Maryland.
  • Mendelsohn L; Sickle Cell Branch, National Heart Lung and Blood Institute, National Institutes of Health, Bethesda, Maryland.
  • Harper J; Laboratory of Chemical Physics, NIDDK National Institutes of Health, Bethesda, Maryland.
  • Ostrowski D; Laboratory of Chemical Physics, NIDDK National Institutes of Health, Bethesda, Maryland.
  • Henry ER; Laboratory of Chemical Physics, NIDDK National Institutes of Health, Bethesda, Maryland.
  • Gwaabe E; Sickle Cell Branch, National Heart Lung and Blood Institute, National Institutes of Health, Bethesda, Maryland.
  • Nichols J; Sickle Cell Branch, National Heart Lung and Blood Institute, National Institutes of Health, Bethesda, Maryland.
  • Alayash AI; Laboratory of Biochemistry and Vascular Biology, Center for Biologics Evaluation and Research, Food and Drug Administration (FDA), Silver Spring, Maryland.
  • Eaton WA; Laboratory of Chemical Physics, NIDDK National Institutes of Health, Bethesda, Maryland.
  • Thein SL; Sickle Cell Branch, National Heart Lung and Blood Institute, National Institutes of Health, Bethesda, Maryland.
Am J Hematol ; 94(4): E88-E90, 2019 04.
Article en En | MEDLINE | ID: mdl-30592074

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Pirazinas / Pirazoles / Benzaldehídos / Anemia de Células Falciformes Límite: Adult / Female / Humans Idioma: En Revista: Am J Hematol Año: 2019 Tipo del documento: Article

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Asunto principal: Pirazinas / Pirazoles / Benzaldehídos / Anemia de Células Falciformes Límite: Adult / Female / Humans Idioma: En Revista: Am J Hematol Año: 2019 Tipo del documento: Article
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