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A Double-Blind, Randomized, Placebo-Controlled Clinical Study of Trofinetide in the Treatment of Fragile X Syndrome.
Berry-Kravis, Elizabeth; Horrigan, Joseph P; Tartaglia, Nicole; Hagerman, Randi; Kolevzon, Alexander; Erickson, Craig A; Hatti, Shivkumar; Snape, Mike; Yaroshinsky, Alex; Stoms, George; Glass, Larry; Jones, Nancy E.
Afiliación
  • Berry-Kravis E; Department of Pediatrics, Rush University Medical Center, Chicago, Illinois; Department of Neurological Sciences, Rush University Medical Center, Chicago, Illinois; Department of Biochemistry, Rush University Medical Center, Chicago, Illinois. Electronic address: Elizabeth_Berry-Kravis@rush.edu.
  • Horrigan JP; Department of Psychiatry and Behavioral Sciences, Duke University, Durham, North Carolina.
  • Tartaglia N; Department of Pediatrics, Children's Hospital Colorado, University of Colorado School of Medicine, Aurora, Colorado.
  • Hagerman R; Department of Pediatrics, University of California Davis MIND Institute, Sacramento, California.
  • Kolevzon A; Division of Child and Adolescent Psychiatry, Department of Pediatrics, Icahn School of Medicine at Mount Sinai, New York, New York; Division of Child and Adolescent Psychiatry, Department of Psychiatry, Icahn School of Medicine at Mount Sinai, New York, New York.
  • Erickson CA; Cincinnati Children's Hospital Medical Center, University of Cincinnati College of Medicine, Cincinnati, Ohio.
  • Hatti S; Suburban Research Associates, Media, Pennsylvania.
  • Snape M; AMO Pharma Ltd., London, UK.
  • Yaroshinsky A; Vital Systems, Inc., Rolling Meadows, Illinois.
  • Stoms G; Vital Systems, Inc., Rolling Meadows, Illinois.
  • Glass L; Neuren Pharmaceuticals, Ltd., Melbourne, Victoria, Australia.
  • Jones NE; Neuren Pharmaceuticals, Ltd., Melbourne, Victoria, Australia.
Pediatr Neurol ; 110: 30-41, 2020 09.
Article en En | MEDLINE | ID: mdl-32660869

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Contexto en salud: 1_ASSA2030 Problema de salud: 1_doencas_nao_transmissiveis Asunto principal: Evaluación de Resultado en la Atención de Salud / Síndrome del Cromosoma X Frágil / Glutamatos Tipo de estudio: Clinical_trials / Prognostic_studies Límite: Adolescent / Adult / Child / Humans / Male Idioma: En Revista: Pediatr Neurol Asunto de la revista: NEUROLOGIA / PEDIATRIA Año: 2020 Tipo del documento: Article

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Contexto en salud: 1_ASSA2030 Problema de salud: 1_doencas_nao_transmissiveis Asunto principal: Evaluación de Resultado en la Atención de Salud / Síndrome del Cromosoma X Frágil / Glutamatos Tipo de estudio: Clinical_trials / Prognostic_studies Límite: Adolescent / Adult / Child / Humans / Male Idioma: En Revista: Pediatr Neurol Asunto de la revista: NEUROLOGIA / PEDIATRIA Año: 2020 Tipo del documento: Article
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