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A novel mouse model of Duchenne muscular dystrophy carrying a multi-exonic Dmd deletion exhibits progressive muscular dystrophy and early-onset cardiomyopathy.
Wong, Tatianna Wai Ying; Ahmed, Abdalla; Yang, Grace; Maino, Eleonora; Steiman, Sydney; Hyatt, Elzbieta; Chan, Parry; Lindsay, Kyle; Wong, Nicole; Golebiowski, Diane; Schneider, Joel; Delgado-Olguín, Paul; Ivakine, Evgueni A; Cohn, Ronald D.
Afiliación
  • Wong TWY; Program in Genetics and Genome Biology, The Hospital for Sick Children Research Institute, Toronto, ON M5G 0A4, Canada.
  • Ahmed A; Department of Molecular Genetics, University of Toronto, Toronto, ON M5S 1A8, Canada.
  • Yang G; Program in Genetics and Genome Biology, The Hospital for Sick Children Research Institute, Toronto, ON M5G 0A4, Canada.
  • Maino E; Program in Translational Medicine, The Hospital for Sick Children Research Institute, Toronto, ON M5G 0A4, Canada.
  • Steiman S; Program in Genetics and Genome Biology, The Hospital for Sick Children Research Institute, Toronto, ON M5G 0A4, Canada.
  • Hyatt E; Program in Genetics and Genome Biology, The Hospital for Sick Children Research Institute, Toronto, ON M5G 0A4, Canada.
  • Chan P; Department of Molecular Genetics, University of Toronto, Toronto, ON M5S 1A8, Canada.
  • Lindsay K; Program in Genetics and Genome Biology, The Hospital for Sick Children Research Institute, Toronto, ON M5G 0A4, Canada.
  • Wong N; Program in Genetics and Genome Biology, The Hospital for Sick Children Research Institute, Toronto, ON M5G 0A4, Canada.
  • Golebiowski D; Program in Genetics and Genome Biology, The Hospital for Sick Children Research Institute, Toronto, ON M5G 0A4, Canada.
  • Schneider J; Program in Genetics and Genome Biology, The Hospital for Sick Children Research Institute, Toronto, ON M5G 0A4, Canada.
  • Delgado-Olguín P; Program in Genetics and Genome Biology, The Hospital for Sick Children Research Institute, Toronto, ON M5G 0A4, Canada.
  • Ivakine EA; Solid Biosciences, Cambridge, MA 02142, USA.
  • Cohn RD; Solid Biosciences, Cambridge, MA 02142, USA.
Dis Model Mech ; 13(9)2020 09 21.
Article en En | MEDLINE | ID: mdl-32988972

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Contexto en salud: 6_ODS3_enfermedades_notrasmisibles Problema de salud: 6_cardiovascular_diseases / 6_other_circulatory_diseases Asunto principal: Exones / Distrofina / Eliminación de Gen / Distrofia Muscular de Duchenne / Cardiomiopatías Límite: Animals Idioma: En Revista: Dis Model Mech Asunto de la revista: MEDICINA Año: 2020 Tipo del documento: Article País de afiliación: Canadá

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Contexto en salud: 6_ODS3_enfermedades_notrasmisibles Problema de salud: 6_cardiovascular_diseases / 6_other_circulatory_diseases Asunto principal: Exones / Distrofina / Eliminación de Gen / Distrofia Muscular de Duchenne / Cardiomiopatías Límite: Animals Idioma: En Revista: Dis Model Mech Asunto de la revista: MEDICINA Año: 2020 Tipo del documento: Article País de afiliación: Canadá
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