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In vivo base editing rescues photoreceptors in a mouse model of retinitis pigmentosa.
Su, Jing; She, Kaiqin; Song, Li; Jin, Xiu; Li, Ruiting; Zhao, Qinyu; Xiao, Jianlu; Chen, Danian; Cheng, Hui; Lu, Fang; Wei, Yuquan; Yang, Yang.
Afiliación
  • Su J; State Key Laboratory of Biotherapy and Cancer Center, West China Hospital, Sichuan University and Collaborative Innovation Center, Chengdu, Sichuan, China.
  • She K; Department of Ophthalmology, West China Hospital, Sichuan University, Chengdu, Sichuan, China.
  • Song L; State Key Laboratory of Biotherapy and Cancer Center, West China Hospital, Sichuan University and Collaborative Innovation Center, Chengdu, Sichuan, China.
  • Jin X; State Key Laboratory of Biotherapy and Cancer Center, West China Hospital, Sichuan University and Collaborative Innovation Center, Chengdu, Sichuan, China.
  • Li R; State Key Laboratory of Biotherapy and Cancer Center, West China Hospital, Sichuan University and Collaborative Innovation Center, Chengdu, Sichuan, China.
  • Zhao Q; State Key Laboratory of Biotherapy and Cancer Center, West China Hospital, Sichuan University and Collaborative Innovation Center, Chengdu, Sichuan, China.
  • Xiao J; State Key Laboratory of Biotherapy and Cancer Center, West China Hospital, Sichuan University and Collaborative Innovation Center, Chengdu, Sichuan, China.
  • Chen D; Research Laboratory of Ophthalmology and Vision Sciences, State Key Laboratory of Biotherapy, West China Hospital, Sichuan University, Chengdu, Sichuan, China.
  • Cheng H; Institute of Rare Diseases, West China Hospital, Sichuan University, Chengdu, Sichuan, China.
  • Lu F; Department of Ophthalmology, West China Hospital, Sichuan University, Chengdu, Sichuan, China.
  • Wei Y; State Key Laboratory of Biotherapy and Cancer Center, West China Hospital, Sichuan University and Collaborative Innovation Center, Chengdu, Sichuan, China.
  • Yang Y; Department of Ophthalmology, West China Hospital, Sichuan University, Chengdu, Sichuan, China.
Mol Ther Nucleic Acids ; 31: 596-609, 2023 Mar 14.
Article en En | MEDLINE | ID: mdl-36910709

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Año: 2023 Tipo del documento: Article País de afiliación: China

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Año: 2023 Tipo del documento: Article País de afiliación: China
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