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Predictors of 6-year event-free survival in Alagille syndrome patients treated with maralixibat, an ileal bile acid transporter inhibitor.
Sokol, Ronald J; Gonzales, Emmanuel M; Kamath, Binita M; Baker, Alastair; Vig, Pamela; Mogul, Douglas B; Garner, Will; Hansen, Bettina E; Jacquemin, Emmanuel; Thompson, Richard J.
Afiliación
  • Sokol RJ; Section of Pediatric Gastroenterology, Hepatology and Nutrition and the Digestive Health Institute, Children's Hospital Colorado and University of Colorado School of Medicine, Aurora, Colorado, USA.
  • Gonzales EM; Department of Pediatric Hepatology and Liver Transplantation, National reference center for biliary atresia and genetic cholestasis (AVB-CG), FSMR FILFOIE, ERN RARE-LIVER, AP-HP, Université Paris-Saclay, Bicêtre Hospital, Le Kremlin-Bicêtre, France.
  • Kamath BM; Department of Pediatric Hepatology and Liver Transplantation, Inserm UMR_S 1193, Université Paris-Saclay, FHU Hepatinov, Orsay, France.
  • Baker A; Department of Pediatrics, Division of Gastroenterology, Hepatology and Nutrition, The Hospital for Sick Children and the University of Toronto, Toronto, Ontario, Canada.
  • Vig P; Pediatric Liver Department, Pediatric Liver Centre, King's College Hospital, London, UK.
  • Mogul DB; Department of Scientific and Medical Affairs, Mirum Pharmaceuticals Inc., Foster City, California, USA.
  • Garner W; Department of Epidemiology, Erasmus MC, Rotterdam, The Netherlands.
  • Hansen BE; Department of Scientific and Medical Affairs, Mirum Pharmaceuticals Inc., Foster City, California, USA.
  • Jacquemin E; Department of Epidemiology, Erasmus MC, Rotterdam, The Netherlands.
  • Thompson RJ; Department of Pediatric Hepatology and Liver Transplantation, National reference center for biliary atresia and genetic cholestasis (AVB-CG), FSMR FILFOIE, ERN RARE-LIVER, AP-HP, Université Paris-Saclay, Bicêtre Hospital, Le Kremlin-Bicêtre, France.
Hepatology ; 78(6): 1698-1710, 2023 Dec 01.
Article en En | MEDLINE | ID: mdl-37278241

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Contexto en salud: 6_ODS3_enfermedades_notrasmisibles Problema de salud: 6_cardiovascular_diseases / 6_congenital_chromosomal_anomalies / 6_digestive_diseases / 6_other_circulatory_diseases Asunto principal: Síndrome de Alagille Tipo de estudio: Prognostic_studies / Risk_factors_studies Límite: Humans Idioma: En Revista: Hepatology Año: 2023 Tipo del documento: Article País de afiliación: Estados Unidos

Texto completo: 1 Colección: 01-internacional Base de datos: MEDLINE Contexto en salud: 6_ODS3_enfermedades_notrasmisibles Problema de salud: 6_cardiovascular_diseases / 6_congenital_chromosomal_anomalies / 6_digestive_diseases / 6_other_circulatory_diseases Asunto principal: Síndrome de Alagille Tipo de estudio: Prognostic_studies / Risk_factors_studies Límite: Humans Idioma: En Revista: Hepatology Año: 2023 Tipo del documento: Article País de afiliación: Estados Unidos
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