Development of an AAV-Based MicroRNA Gene Therapy to Treat Machado-Joseph Disease.

Martier, Raygene; Sogorb-Gonzalez, Marina; Stricker-Shaver, Janice; Hübener-Schmid, Jeannette; Keskin, Sonay; Klima, Jiri; Toonen, Lodewijk J; Juhas, Stefan; Juhasova, Jana; Ellederova, Zdenka; Motlik, Jan; Haas, Eva; van Deventer, Sander; Konstantinova, Pavlina; Nguyen, Huu Phuc; Evers, Melvin M

Martier, Raygene; Sogorb-Gonzalez, Marina; Stricker-Shaver, Janice; Hübener-Schmid, Jeannette; Keskin, Sonay; Klima, Jiri; Toonen, Lodewijk J; Juhas, Stefan; Juhasova, Jana; Ellederova, Zdenka; Motlik, Jan; Haas, Eva; van Deventer, Sander; Konstantinova, Pavlina; Nguyen, Huu Phuc; Evers, Melvin M.

Afiliação

Martier R; Department of Research & Development, uniQure Biopharma B.V., Amsterdam, the Netherlands.
Sogorb-Gonzalez M; Department of Gastroenterology and Hepatology, Leiden University Medical Center, Leiden, the Netherlands.
Stricker-Shaver J; Department of Research & Development, uniQure Biopharma B.V., Amsterdam, the Netherlands.
Hübener-Schmid J; Department of Gastroenterology and Hepatology, Leiden University Medical Center, Leiden, the Netherlands.
Keskin S; Institute of Medical Genetics and Applied Genomics, University of Tuebingen, Tuebingen, Germany.
Klima J; Institute of Medical Genetics and Applied Genomics, University of Tuebingen, Tuebingen, Germany.
Toonen LJ; Department of Research & Development, uniQure Biopharma B.V., Amsterdam, the Netherlands.
Juhas S; Institute of Animal Physiology and Genetics, Libechov, Czech Republic.
Juhasova J; Department of Research & Development, uniQure Biopharma B.V., Amsterdam, the Netherlands.
Ellederova Z; Institute of Animal Physiology and Genetics, Libechov, Czech Republic.
Motlik J; Institute of Animal Physiology and Genetics, Libechov, Czech Republic.
Haas E; Institute of Animal Physiology and Genetics, Libechov, Czech Republic.
van Deventer S; Institute of Animal Physiology and Genetics, Libechov, Czech Republic.
Konstantinova P; Institute of Medical Genetics and Applied Genomics, University of Tuebingen, Tuebingen, Germany.
Nguyen HP; Department of Research & Development, uniQure Biopharma B.V., Amsterdam, the Netherlands.
Evers MM; Department of Gastroenterology and Hepatology, Leiden University Medical Center, Leiden, the Netherlands.

Mol Ther Methods Clin Dev ; 15: 343-358, 2019 Dec 13.

Article em En | MEDLINE | ID: mdl-31828177

Texto completo

Adicionar na Minha BVS

Imprimir

XML

PubMed Links

Buscar no Google

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Prognostic_studies Idioma: En Revista: Mol Ther Methods Clin Dev Ano de publicação: 2019 Tipo de documento: Article País de afiliação: Holanda

Texto completo

Adicionar na Minha BVS

Imprimir

XML

PubMed Links

Buscar no Google