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Clinical features and outcomes of patients with Shwachman-Diamond syndrome and myelodysplastic syndrome or acute myeloid leukaemia: a multicentre, retrospective, cohort study.
Myers, Kasiani C; Furutani, Elissa; Weller, Edie; Siegele, Bradford; Galvin, Ashley; Arsenault, Valerie; Alter, Blanche P; Boulad, Farid; Bueso-Ramos, Carlos; Burroughs, Lauri; Castillo, Paul; Connelly, James; Davies, Stella M; DiNardo, Courtney D; Hanif, Iftikhar; Ho, Richard H; Karras, Nicole; Manalang, Michelle; McReynolds, Lisa J; Nakano, Taizo A; Nalepa, Grzegorz; Norkin, Maxim; Oberley, Matthew J; Orgel, Etan; Pastore, Yves D; Rosenthal, Joseph; Walkovich, Kelly; Larson, Jordan; Malsch, Maggie; Elghetany, M Tarek; Fleming, Mark D; Shimamura, Akiko.
Afiliação
  • Myers KC; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, OH, USA; Division of Bone Marrow Transplantation and Immune Deficiency, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA; Division of Bone Marrow Transplantation and Immune Deficiency, Cincinnati Ch
  • Furutani E; Pediatric Hematology-Oncology, Boston Children's Hospital, Boston, MA, USA; Dana Farber Cancer Institute, Boston, MA, USA; Department of Pediatrics, Harvard Medical School, Boston, MA, USA.
  • Weller E; Division of Hematology and Oncology and Biostatistics and Research Design Center, Institutional Centers for Clinical and Translational Research, Boston Children's Hospital, Boston, MA, USA.
  • Siegele B; Department of Pathology, Boston Children's Hospital, Boston, MA, USA.
  • Galvin A; Pediatric Hematology-Oncology, Boston Children's Hospital, Boston, MA, USA.
  • Arsenault V; CHU Sainte-Justine, University of Montreal, Montreal, QC, Canada.
  • Alter BP; Clinical Genetics Branch, National Institutes of Health National Cancer Institute, Rockville, MD, USA.
  • Boulad F; Department of Pediatrics, Bone Marrow Transplantation Service, Memorial Sloan Kettering Cancer Center, New York, NY, USA.
  • Bueso-Ramos C; Department of Hematopathology, The University of Texas MD Anderson Cancer Center, Houston, TX, USA.
  • Burroughs L; Department of Pediatrics, Division of Hematology-Oncology Seattle Children's and Clinical Research Division, Fred Hutchinson Cancer Research Center, Seattle, WA, USA.
  • Castillo P; Shands Children's Hospital, Department of Pediatrics, Division of Pediatric Hematology Oncology, University of Florida, Gainesville, FL, USA.
  • Connelly J; Department of Pediatrics, Division of Pediatric Hematology Oncology, Vanderbilt University Medical Center, Nashville, TN, USA.
  • Davies SM; Department of Pediatrics, University of Cincinnati College of Medicine, Cincinnati, OH, USA; Division of Bone Marrow Transplantation and Immune Deficiency, Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
  • DiNardo CD; Department of Leukemia, The University of Texas MD Anderson Cancer Center, Houston, TX, USA.
  • Hanif I; Center for Cancer and Blood Disorders, Joe DiMaggio Children's Hospital, Hollywood, FL, USA.
  • Ho RH; Department of Pediatrics, Division of Pediatric Hematology Oncology, Vanderbilt University Medical Center, Nashville, TN, USA.
  • Karras N; Department of Pediatrics, City of Hope National Medical Center, Duarte, CA, USA.
  • Manalang M; Marshfield Clinic Health System, Marshfield, WI, USA.
  • McReynolds LJ; Clinical Genetics Branch, National Institutes of Health National Cancer Institute, Rockville, MD, USA.
  • Nakano TA; Center for Cancer and Blood Disorders, Children's Hospital Colorado, University of Colorado School of Medicine, Aurora, CO, USA.
  • Nalepa G; Department of Pediatrics, Division of Pediatric Hematology-Oncology, Indiana University School of Medicine, Indianapolis, IN, USA.
  • Norkin M; Department of Medicine, University of Florida, Gainesville, FL, USA.
  • Oberley MJ; Department of Pathology and Laboratory Medicine, Children's Hospital Los Angeles, Keck School of Medicine, University of Southern California, Los Angeles, CA, USA.
  • Orgel E; Division of Pediatric Hematology Oncology and Blood and Marrow Transplantation, Children's Hospital Los Angeles, Keck School of Medicine, University of Southern California, Los Angeles, CA, USA.
  • Pastore YD; CHU Sainte-Justine, University of Montreal, Montreal, QC, Canada.
  • Rosenthal J; Department of Pediatrics, City of Hope National Medical Center, Duarte, CA, USA; Department of Pediatrics, City of Hope National Medical Center, Duarte, CA, USA.
  • Walkovich K; Division of Pediatric Hematology- Oncology, Department of Pediatrics, University of Michigan Medical School, Ann Arbor, MI, USA.
  • Larson J; Pediatric Hematology-Oncology, Boston Children's Hospital, Boston, MA, USA.
  • Malsch M; Pediatric Hematology-Oncology, Boston Children's Hospital, Boston, MA, USA.
  • Elghetany MT; Department of Pathology and Immunology, Baylor College of Medicine, Houston, TX, USA.
  • Fleming MD; Department of Pathology, Boston Children's Hospital, Boston, MA, USA.
  • Shimamura A; Pediatric Hematology-Oncology, Boston Children's Hospital, Boston, MA, USA; Dana Farber Cancer Institute, Boston, MA, USA; Department of Pediatrics, Harvard Medical School, Boston, MA, USA. Electronic address: akiko.shimamura@childrens.harvard.edu.
Lancet Haematol ; 7(3): e238-e246, 2020 Mar.
Article em En | MEDLINE | ID: mdl-31879230

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Contexto em Saúde: 2_ODS3 / 6_ODS3_enfermedades_notrasmisibles / 7_ODS3_muertes_prevenibles_nacidos_ninos Problema de saúde: 2_muertes_prevenibles / 6_endocrine_disorders / 6_leukemia / 7_non_communicable_diseases Assunto principal: Síndromes Mielodisplásicas / Leucemia Mieloide Aguda / Protocolos de Quimioterapia Combinada Antineoplásica / Transplante de Células-Tronco Hematopoéticas / Síndrome de Shwachman-Diamond Tipo de estudo: Etiology_studies / Guideline / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Adult / Child / Child, preschool / Female / Humans / Infant / Male / Middle aged / Newborn Idioma: En Revista: Lancet Haematol Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Contexto em Saúde: 2_ODS3 / 6_ODS3_enfermedades_notrasmisibles / 7_ODS3_muertes_prevenibles_nacidos_ninos Problema de saúde: 2_muertes_prevenibles / 6_endocrine_disorders / 6_leukemia / 7_non_communicable_diseases Assunto principal: Síndromes Mielodisplásicas / Leucemia Mieloide Aguda / Protocolos de Quimioterapia Combinada Antineoplásica / Transplante de Células-Tronco Hematopoéticas / Síndrome de Shwachman-Diamond Tipo de estudo: Etiology_studies / Guideline / Observational_studies / Prognostic_studies / Risk_factors_studies Limite: Adolescent / Adult / Child / Child, preschool / Female / Humans / Infant / Male / Middle aged / Newborn Idioma: En Revista: Lancet Haematol Ano de publicação: 2020 Tipo de documento: Article
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