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Emapalumab treatment in an ADA-SCID patient with refractory hemophagocytic lymphohistiocytosis-related graft failure and disseminated bacillus Calmette-Guérin infection.
Tucci, Francesca; Gallo, Vera; Barzaghi, Federica; Ferrua, Francesca; Migliavacca, Maddalena; Calbi, Valeria; Doglio, Matteo; Fratini, Elena Sophia; Karakas, Zeynep; Guner, Sukru; Zambelli, Matilde; Parisi, Cristina; Milani, Raffaella; Gattillo, Salvatore; Mazzi, Benedetta; Oltolini, Chiara; Barbera, Maurizio; Baldoli, Cristina; Cirillo, Daniela Maria; Asnaghi, Veronica; De Min, Cristina; Cicalese, Maria Pia; Ciceri, Fabio; Aiuti, Alessandro; Bernardo, Maria Ester.
Afiliação
  • Tucci F; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Gallo V; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Barzaghi F; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Ferrua F; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Migliavacca M; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Calbi V; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Doglio M; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Fratini ES; Pediatric Immunohematology Unit and BMT Program, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Karakas Z; Division of Hematology and Oncology, Istanbul University, Faculty of Medicine, Istanbul, Turkey.
  • Guner S; Department of Pediatrics, Division of Immunology and Allergy, Necmettin Erbakan University Faculty of Medicine, Konya, Turkey.
  • Zambelli M; Immunohematology and Transfusion Medicine Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Parisi C; Immunohematology and Transfusion Medicine Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Milani R; Immunohematology and Transfusion Medicine Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Gattillo S; Immunohematology and Transfusion Medicine Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Mazzi B; Immunogenetics, HLA and Chimerism Laboratory, IRCCS San Raffaele Scientific Institute, Milano, Italy.
  • Oltolini C; IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Barbera M; IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Baldoli C; IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Cirillo DM; IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Asnaghi V; Swedish Orphan Biovitrum AG (Sobi), Basel, Switzerland.
  • De Min C; Swedish Orphan Biovitrum AG (Sobi), Basel, Switzerland.
  • Cicalese MP; IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Ciceri F; Vita-Salute San Raffaele University Milan, Italy.
  • Aiuti A; IRCCS San Raffaele Scientific Institute, Milan, Italy.
  • Bernardo ME; IRCCS San Raffaele Scientific Institute, Milan, Italy.
Haematologica ; 106(2): 641-646, 2021 02 01.
Article em En | MEDLINE | ID: mdl-32817285

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Contexto em Saúde: 2_ODS3 / 3_ND Problema de saúde: 2_enfermedades_transmissibles / 3_neglected_diseases / 3_tuberculosis / 3_zoonosis Assunto principal: Tuberculose / Imunodeficiência Combinada Severa / Transplante de Células-Tronco Hematopoéticas / Linfo-Histiocitose Hemofagocítica Tipo de estudo: Etiology_studies Limite: Child, preschool / Female / Humans Idioma: En Revista: Haematologica Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Itália

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Contexto em Saúde: 2_ODS3 / 3_ND Problema de saúde: 2_enfermedades_transmissibles / 3_neglected_diseases / 3_tuberculosis / 3_zoonosis Assunto principal: Tuberculose / Imunodeficiência Combinada Severa / Transplante de Células-Tronco Hematopoéticas / Linfo-Histiocitose Hemofagocítica Tipo de estudo: Etiology_studies Limite: Child, preschool / Female / Humans Idioma: En Revista: Haematologica Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Itália
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