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Evidence of feedback regulation of C-type natriuretic peptide during Vosoritide therapy in Achondroplasia.
Prickett, Timothy C R; Espiner, Eric A; Irving, Melita; Bacino, Carlos; Phillips, John A; Savarirayan, Ravi; Day, Jonathan R S; Fisheleva, Elena; Larimore, Kevin; Chan, Ming Liang; Jeha, George S.
Afiliação
  • Prickett TCR; Department of Medicine, University of Otago, Christchurch, PO Box 4345, Christchurch, 8140, New Zealand. tim.prickett@otago.ac.nz.
  • Espiner EA; Department of Medicine, University of Otago, Christchurch, PO Box 4345, Christchurch, 8140, New Zealand.
  • Irving M; Guy's and St. Thomas' NHS Foundation Trust, Evelina Children's Hospital, London, UK.
  • Bacino C; Baylor College of Medicine, Houston, TX, USA.
  • Phillips JA; Vanderbilt University Medical Center, Nashville, TN, USA.
  • Savarirayan R; Murdoch Children's Research Institute, Royal Children's Hospital Victoria, University of Melbourne, Parkville, VIC, Australia.
  • Day JRS; BioMarin Pharmaceutical, Novato, CA, USA.
  • Fisheleva E; BioMarin Pharmaceutical, Novato, CA, USA.
  • Larimore K; BioMarin Pharmaceutical, Novato, CA, USA.
  • Chan ML; BioMarin Pharmaceutical, Novato, CA, USA.
  • Jeha GS; BioMarin Pharmaceutical, Novato, CA, USA.
Sci Rep ; 11(1): 24278, 2021 12 20.
Article em En | MEDLINE | ID: mdl-34930956

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Acondroplasia / Peptídeo Natriurético Tipo C Limite: Adolescent / Child / Child, preschool / Female / Humans / Male Idioma: En Revista: Sci Rep Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Nova Zelândia

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Acondroplasia / Peptídeo Natriurético Tipo C Limite: Adolescent / Child / Child, preschool / Female / Humans / Male Idioma: En Revista: Sci Rep Ano de publicação: 2021 Tipo de documento: Article País de afiliação: Nova Zelândia
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