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Lentiviral Mediated ADA2 Gene Transfer Corrects the Defects Associated With Deficiency of Adenosine Deaminase Type 2.
Hong, Ying; Casimir, Marina; Houghton, Benjamin C; Zhang, Fang; Jensen, Barbara; Omoyinmi, Ebun; Torrance, Robert; Papadopoulou, Charalampia; Cummins, Michelle; Roderick, Marion; Thrasher, Adrian J; Brogan, Paul A; Eleftheriou, Despina.
Afiliação
  • Hong Y; Infection, Immunity, Inflammation Department, University College London (UCL) Great Ormond Street Institute of Child Health, London, United Kingdom.
  • Casimir M; Infection, Immunity, Inflammation Department, University College London (UCL) Great Ormond Street Institute of Child Health, London, United Kingdom.
  • Houghton BC; Infection, Immunity, Inflammation Department, University College London (UCL) Great Ormond Street Institute of Child Health, London, United Kingdom.
  • Zhang F; Infection, Immunity, Inflammation Department, University College London (UCL) Great Ormond Street Institute of Child Health, London, United Kingdom.
  • Jensen B; Infection, Immunity, Inflammation Department, University College London (UCL) Great Ormond Street Institute of Child Health, London, United Kingdom.
  • Omoyinmi E; Infection, Immunity, Inflammation Department, University College London (UCL) Great Ormond Street Institute of Child Health, London, United Kingdom.
  • Torrance R; Infection, Immunity, Inflammation Department, University College London (UCL) Great Ormond Street Institute of Child Health, London, United Kingdom.
  • Papadopoulou C; Infection, Immunity, Inflammation Department, University College London (UCL) Great Ormond Street Institute of Child Health, London, United Kingdom.
  • Cummins M; Paediatric Haematology, Bristol Royal Hospital for Children, Bristol, United Kingdom.
  • Roderick M; Paediatric Clinical Immunology, Bristol Royal Hospital for Children, Bristol, United Kingdom.
  • Thrasher AJ; Infection, Immunity, Inflammation Department, University College London (UCL) Great Ormond Street Institute of Child Health, London, United Kingdom.
  • Brogan PA; Infection, Immunity, Inflammation Department, University College London (UCL) Great Ormond Street Institute of Child Health, London, United Kingdom.
  • Eleftheriou D; Infection, Immunity, Inflammation Department, University College London (UCL) Great Ormond Street Institute of Child Health, London, United Kingdom.
Front Immunol ; 13: 852830, 2022.
Article em En | MEDLINE | ID: mdl-35529868

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Vasculite / Terapia Genética / Imunodeficiência Combinada Severa / Agamaglobulinemia Tipo de estudo: Prognostic_studies / Risk_factors_studies Limite: Humans Idioma: En Revista: Front Immunol Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Reino Unido

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Vasculite / Terapia Genética / Imunodeficiência Combinada Severa / Agamaglobulinemia Tipo de estudo: Prognostic_studies / Risk_factors_studies Limite: Humans Idioma: En Revista: Front Immunol Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Reino Unido
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