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Orphan Drug Use in Patients With Rare Diseases: A Population-Based Cohort Study.
Gorini, Francesca; Santoro, Michele; Pierini, Anna; Mezzasalma, Lorena; Baldacci, Silvia; Bargagli, Elena; Boncristiano, Alessandra; Brunetto, Maurizia Rossana; Cameli, Paolo; Cappelli, Francesco; Castaman, Giancarlo; Coco, Barbara; Donati, Maria Alice; Guerrini, Renzo; Linari, Silvia; Murro, Vittoria; Olivotto, Iacopo; Parronchi, Paola; Pochiero, Francesca; Rossi, Oliviero; Scappini, Barbara; Sodi, Andrea; Vannucchi, Alessandro Maria; Coi, Alessio.
Afiliação
  • Gorini F; Unit of Epidemiology of Rare Diseases and Congenital Anomalies, Institute of Clinical Physiology, National Research Council, Pisa, Italy.
  • Santoro M; Unit of Epidemiology of Rare Diseases and Congenital Anomalies, Institute of Clinical Physiology, National Research Council, Pisa, Italy.
  • Pierini A; Unit of Epidemiology of Rare Diseases and Congenital Anomalies, Institute of Clinical Physiology, National Research Council, Pisa, Italy.
  • Mezzasalma L; Unit of Epidemiology of Rare Diseases and Congenital Anomalies, Institute of Clinical Physiology, National Research Council, Pisa, Italy.
  • Baldacci S; Unit of Epidemiology of Rare Diseases and Congenital Anomalies, Institute of Clinical Physiology, National Research Council, Pisa, Italy.
  • Bargagli E; Respiratory Diseases Unit, Department of Medical and Surgical Sciences and Neurosciences, University of Siena, Siena, Italy.
  • Boncristiano A; Neuroscience Department, A. Meyer Children Hospital-University of Florence, Florence, Italy.
  • Brunetto MR; Department of Clinical and Experimental Medicine, University of Pisa, Pisa, Italy.
  • Cameli P; Respiratory Diseases Unit, Department of Medical and Surgical Sciences and Neurosciences, University of Siena, Siena, Italy.
  • Cappelli F; Cardiomyopathy Unit, Careggi University Hospital, University of Florence, Florence, Italy.
  • Castaman G; Center for Bleeding Disorders and Coagulation, Department of Oncology, Careggi University Hospital, Florence, Italy.
  • Coco B; Hepatology Unit, University Hospital of Pisa, Pisa, Italy.
  • Donati MA; Metabolic and Muscular Unit, A. Meyer Children Hospital, Florence, Italy.
  • Guerrini R; Neuroscience Department, A. Meyer Children Hospital-University of Florence, Florence, Italy.
  • Linari S; Center for Bleeding Disorders and Coagulation, Department of Oncology, Careggi University Hospital, Florence, Italy.
  • Murro V; Department of Neuroscience, Psychology, Drug Research and Child Health, University of Florence, Careggi University Hospital, Florence, Italy.
  • Olivotto I; Cardiomyopathy Unit, Careggi University Hospital, University of Florence, Florence, Italy.
  • Parronchi P; Department of Experimental and Clinical Medicine, SOD Immunologia e Terapie Cellulari, Careggi University Hospital, University of Florence, Florence, Italy.
  • Pochiero F; Metabolic and Muscular Unit, A. Meyer Children Hospital, Florence, Italy.
  • Rossi O; Immunuallergology Unit, SOD Immunoallergologia, Careggi University Hospital, Florence, Italy.
  • Scappini B; Hematology Unit, Careggi University Hospital, Florence, Italy.
  • Sodi A; Department of Neuroscience, Psychology, Drug Research and Child Health, University of Florence, Careggi University Hospital, Florence, Italy.
  • Vannucchi AM; Center Research and Innovation of Myeloproliferative Neoplasms (CRIMM), Department of Experimental and Clinical Medicine, Careggi University Hospital, University of Florence, Florence, Italy.
  • Coi A; Unit of Epidemiology of Rare Diseases and Congenital Anomalies, Institute of Clinical Physiology, National Research Council, Pisa, Italy.
Front Pharmacol ; 13: 869842, 2022.
Article em En | MEDLINE | ID: mdl-35652051

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Etiology_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Idioma: En Revista: Front Pharmacol Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Itália

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Etiology_studies / Observational_studies / Prognostic_studies / Risk_factors_studies Idioma: En Revista: Front Pharmacol Ano de publicação: 2022 Tipo de documento: Article País de afiliação: Itália
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