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Augmentation Therapy for Severe Alpha-1 Antitrypsin Deficiency Improves Survival and Is Decoupled from Spirometric Decline-A Multinational Registry Analysis.
Fraughen, Daniel D; Ghosh, Auyon J; Hobbs, Brian D; Funk, Georg-Christian; Meischl, Tobias; Clarenbach, Christian F; Sievi, Noriane A; Schmid-Scherzer, Karin; McElvaney, Oliver J; Murphy, Mark P; Roche, Adam D; Clarke, Louise; Strand, Matthew; Vafai-Tabrizi, Florian; Kelly, Geraldine; Gunaratnam, Cedric; Carroll, Tomás P; McElvaney, Noel G.
Afiliação
  • Fraughen DD; Department of Medicine, Irish Center for Genetic Lung Disease, Royal College of Surgeons in Ireland, Dublin, Ireland.
  • Ghosh AJ; Division of Pulmonary, Critical Care, and Sleep Medicine, SUNY Upstate University Hospital, Syracuse, New York.
  • Hobbs BD; Channing Division of Network Medicine and Division of Pulmonary and Critical Care Medicine, Brigham and Women's Hospital, Boston, Massachusetts.
  • Funk GC; Karl Landsteiner Institute for Lung Research and Pulmonary Oncology and Department of Medicine II with Pneumology, Klinik Ottakring, Vienna, Austria.
  • Meischl T; Karl Landsteiner Institute for Lung Research and Pulmonary Oncology and Department of Medicine II with Pneumology, Klinik Ottakring, Vienna, Austria.
  • Clarenbach CF; Division of Gastroenterology and Hepatology, Department of Medicine III, Medical University of Vienna, Vienna, Austria.
  • Sievi NA; Department of Pneumology, University Hospital Zurich, Zurich, Switzerland.
  • Schmid-Scherzer K; Department of Pneumology, University Hospital Zurich, Zurich, Switzerland.
  • McElvaney OJ; Karl Landsteiner Institute for Lung Research and Pulmonary Oncology and Department of Medicine II with Pneumology, Klinik Ottakring, Vienna, Austria.
  • Murphy MP; Department of Medicine, Irish Center for Genetic Lung Disease, Royal College of Surgeons in Ireland, Dublin, Ireland.
  • Roche AD; Division of Pulmonary, Critical Care and Sleep Medicine, University of Washington, Seattle, Washington.
  • Clarke L; Department of Medicine, Irish Center for Genetic Lung Disease, Royal College of Surgeons in Ireland, Dublin, Ireland.
  • Strand M; Department of Medicine, Irish Center for Genetic Lung Disease, Royal College of Surgeons in Ireland, Dublin, Ireland.
  • Vafai-Tabrizi F; Department of Respiratory Physiology, Beaumont Hospital, Dublin, Ireland; and.
  • Kelly G; Division of Biostatistics and Bioinformatics, National Jewish Health, Denver, Colorado.
  • Gunaratnam C; Karl Landsteiner Institute for Lung Research and Pulmonary Oncology and Department of Medicine II with Pneumology, Klinik Ottakring, Vienna, Austria.
  • Carroll TP; Department of Medicine, Irish Center for Genetic Lung Disease, Royal College of Surgeons in Ireland, Dublin, Ireland.
  • McElvaney NG; Department of Respiratory Physiology, Beaumont Hospital, Dublin, Ireland; and.
Am J Respir Crit Care Med ; 208(9): 964-974, 2023 11 01.
Article em En | MEDLINE | ID: mdl-37624745

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Contexto em Saúde: 1_ASSA2030 / 2_ODS3 / 6_ODS3_enfermedades_notrasmisibles Problema de saúde: 1_doencas_nao_transmissiveis / 2_muertes_prematuras_enfermedades_notrasmisibles / 6_chronic_obstructive_pulmonary_disease / 6_digestive_diseases / 6_other_respiratory_diseases Assunto principal: Deficiência de alfa 1-Antitripsina / Doença Pulmonar Obstrutiva Crônica Tipo de estudo: Guideline / Observational_studies Limite: Adult / Humans / Middle aged Idioma: En Revista: Am J Respir Crit Care Med Assunto da revista: TERAPIA INTENSIVA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Irlanda

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Contexto em Saúde: 1_ASSA2030 / 2_ODS3 / 6_ODS3_enfermedades_notrasmisibles Problema de saúde: 1_doencas_nao_transmissiveis / 2_muertes_prematuras_enfermedades_notrasmisibles / 6_chronic_obstructive_pulmonary_disease / 6_digestive_diseases / 6_other_respiratory_diseases Assunto principal: Deficiência de alfa 1-Antitripsina / Doença Pulmonar Obstrutiva Crônica Tipo de estudo: Guideline / Observational_studies Limite: Adult / Humans / Middle aged Idioma: En Revista: Am J Respir Crit Care Med Assunto da revista: TERAPIA INTENSIVA Ano de publicação: 2023 Tipo de documento: Article País de afiliação: Irlanda
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