Your browser doesn't support javascript.
loading
Continued safety and long-term effectiveness of onasemnogene abeparvovec in Ohio.
Waldrop, Megan A; Chagat, Shannon; Storey, Michael; Meyer, Alayne; Iammarino, Megan; Reash, Natalie; Alfano, Lindsay; Lowes, Linda; Noritz, Garey; Prochoroff, Andre; Rossman, Ian; Ginsberg, Matthew; Mosher, Kathryn; Broomall, Eileen; Bass, Nancy; Gushue, Courtney; Kotha, Kavitha; Paul, Grace; Shell, Richard; Tsao, Chang-Yong; Mendell, Jerry R; Connolly, Anne M.
Afiliação
  • Waldrop MA; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus OH, 43205, USA; Departments of Pediatrics and Neurology, Ohio State University Wexner Medical Center, Columbus OH, 43205, USA. Electronic address: megan.waldrop@nationwidechildrens.org.
  • Chagat S; Department of Neurology, Nationwide Children's Hospital, Columbus, OH 43205, USA.
  • Storey M; Department of Pharmacy, Nationwide Children's Hospital, Columbus, OH 43205, USA.
  • Meyer A; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus OH, 43205, USA.
  • Iammarino M; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus OH, 43205, USA.
  • Reash N; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus OH, 43205, USA.
  • Alfano L; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus OH, 43205, USA.
  • Lowes L; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus OH, 43205, USA.
  • Noritz G; Department of Pediatrics, Nationwide Children's hospital, Columbus, OH 43205, USA.
  • Prochoroff A; Department of Pediatric Neurology, Metro Health, Cleveland OH, USA.
  • Rossman I; Department of Pediatric Neurology, Akron Children's Hospital, Akron OH, USA.
  • Ginsberg M; Department of Pediatric Neurology, Akron Children's Hospital, Akron OH, USA.
  • Mosher K; Department of Pediatric Physiatry, Akron Children's Hospital, Akron OH, USA.
  • Broomall E; Department of Pediatric Neurology, Cincinnati Children's Hospital Medical Center, Cincinnati OH, USA.
  • Bass N; Division of Pediatric Neurology, Department of Pediatrics, Rainbow Babies and Children's Hospital, Cleveland OH, USA.
  • Gushue C; Departments of Pediatrics and Pulmonology, Ohio State University Wexner Medical Center, Columbus OH 43205, USA.
  • Kotha K; Departments of Pediatrics and Pulmonology, Ohio State University Wexner Medical Center, Columbus OH 43205, USA.
  • Paul G; Departments of Pediatrics and Pulmonology, Ohio State University Wexner Medical Center, Columbus OH 43205, USA.
  • Shell R; Departments of Pediatrics and Pulmonology, Ohio State University Wexner Medical Center, Columbus OH 43205, USA.
  • Tsao CY; Departments of Pediatrics and Neurology, Ohio State University Wexner Medical Center, Columbus OH, 43205, USA.
  • Mendell JR; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus OH, 43205, USA; Departments of Pediatrics and Neurology, Ohio State University Wexner Medical Center, Columbus OH, 43205, USA.
  • Connolly AM; Center for Gene Therapy, Abigail Wexner Research Institute, Nationwide Children's Hospital, Columbus OH, 43205, USA; Departments of Pediatrics and Neurology, Ohio State University Wexner Medical Center, Columbus OH, 43205, USA.
Neuromuscul Disord ; 34: 41-48, 2024 Jan.
Article em En | MEDLINE | ID: mdl-38142474

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Produtos Biológicos / Proteínas Recombinantes de Fusão / Atrofia Muscular Espinal / Atrofias Musculares Espinais da Infância / Doenças Neurodegenerativas Limite: Child / Humans País/Região como assunto: America do norte Idioma: En Revista: Neuromuscul Disord Assunto da revista: NEUROLOGIA Ano de publicação: 2024 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Produtos Biológicos / Proteínas Recombinantes de Fusão / Atrofia Muscular Espinal / Atrofias Musculares Espinais da Infância / Doenças Neurodegenerativas Limite: Child / Humans País/Região como assunto: America do norte Idioma: En Revista: Neuromuscul Disord Assunto da revista: NEUROLOGIA Ano de publicação: 2024 Tipo de documento: Article
...