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Experience of patisiran with transthyretin stabilizers in patients with hereditary transthyretin-mediated amyloidosis.
Lin, Hollis; Merkel, Madeline; Hale, Cecilia; Marantz, Jing L.
Affiliation
  • Lin H; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.
  • Merkel M; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.
  • Hale C; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.
  • Marantz JL; Alnylam Pharmaceuticals, Cambridge, MA 02142, USA.
Neurodegener Dis Manag ; 10(5): 289-300, 2020 10.
Article in En | MEDLINE | ID: mdl-32519928

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Benzoxazoles / Diflunisal / Amyloid Neuropathies, Familial / RNA, Small Interfering Type of study: Clinical_trials Aspects: Patient_preference Limits: Adult / Aged / Female / Humans / Male / Middle aged Language: En Journal: Neurodegener Dis Manag Year: 2020 Document type: Article

Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Benzoxazoles / Diflunisal / Amyloid Neuropathies, Familial / RNA, Small Interfering Type of study: Clinical_trials Aspects: Patient_preference Limits: Adult / Aged / Female / Humans / Male / Middle aged Language: En Journal: Neurodegener Dis Manag Year: 2020 Document type: Article