Experience of patisiran with transthyretin stabilizers in patients with hereditary transthyretin-mediated amyloidosis.
Neurodegener Dis Manag
; 10(5): 289-300, 2020 10.
Article
in En
| MEDLINE
| ID: mdl-32519928
Key words
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Benzoxazoles
/
Diflunisal
/
Amyloid Neuropathies, Familial
/
RNA, Small Interfering
Type of study:
Clinical_trials
Aspects:
Patient_preference
Limits:
Adult
/
Aged
/
Female
/
Humans
/
Male
/
Middle aged
Language:
En
Journal:
Neurodegener Dis Manag
Year:
2020
Document type:
Article