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Inhaled mRNA therapy for treatment of cystic fibrosis: Interim results of a randomized, double-blind, placebo-controlled phase 1/2 clinical study.
Rowe, S M; Zuckerman, J B; Dorgan, D; Lascano, J; McCoy, K; Jain, M; Schechter, M S; Lommatzsch, S; Indihar, V; Lechtzin, N; McBennett, K; Callison, C; Brown, C; Liou, T G; MacDonald, K D; Nasr, S Z; Bodie, S; Vaughn, M; Meltzer, E B; Barbier, A J.
Affiliation
  • Rowe SM; University of Alabama at Birmingham, USA.
  • Zuckerman JB; Maine Medical Center, Tufts University, USA. Electronic address: jzuckerman@cmamaine.com.
  • Dorgan D; Perelman School of Medicine, University of Pennsylvania, USA.
  • Lascano J; University of Florida, Gainesville, USA.
  • McCoy K; Nationwide Children's Hospital/the Ohio State University, USA.
  • Jain M; Northwestern University Feinberg School of Medicine, USA.
  • Schechter MS; Children's Hospital of Richmond at Virginia Commonwealth University, USA.
  • Lommatzsch S; National Jewish Health, USA.
  • Indihar V; University of Cincinnati, USA.
  • Lechtzin N; Johns Hopkins University, USA.
  • McBennett K; University Hospitals, Cleveland Medical Center, USA.
  • Callison C; University of Tennessee Medical Center, Knoxville, USA.
  • Brown C; Indiana University School of Medicine, USA.
  • Liou TG; University of Utah, Salt Lake City, USA.
  • MacDonald KD; Oregon Health & Science University, USA.
  • Nasr SZ; University of Michigan, Ann Arbor, USA.
  • Bodie S; Translate Bio Inc, Lexington, MA, USA.
  • Vaughn M; Translate Bio Inc, Lexington, MA, USA.
  • Meltzer EB; Translate Bio Inc, Lexington, MA, USA.
  • Barbier AJ; Translate Bio Inc, Lexington, MA, USA.
J Cyst Fibros ; 22(4): 656-664, 2023 07.
Article in En | MEDLINE | ID: mdl-37121795

Full text: 1 Collection: 01-internacional Health context: 1_ASSA2030 Database: MEDLINE Main subject: Cystic Fibrosis Type of study: Clinical_trials / Diagnostic_studies Limits: Adult / Humans Language: En Journal: J Cyst Fibros Year: 2023 Document type: Article

Full text: 1 Collection: 01-internacional Health context: 1_ASSA2030 Database: MEDLINE Main subject: Cystic Fibrosis Type of study: Clinical_trials / Diagnostic_studies Limits: Adult / Humans Language: En Journal: J Cyst Fibros Year: 2023 Document type: Article