On emerging enzyme replacement therapies for neuronopathic mucopolysaccharidosis II.
Mol Genet Metab
; 141(3): 108143, 2024 Mar.
Article
in En
| MEDLINE
| ID: mdl-38277987
Full text:
1
Collection:
01-internacional
Database:
MEDLINE
Main subject:
Mucopolysaccharidosis II
Limits:
Humans
Language:
En
Journal:
Mol Genet Metab
Year:
2024
Document type:
Article