Targeting RNA opens therapeutic avenues for Timothy syndrome.

Velasco, Silvia

Velasco, Silvia.

Nature ; 628(8009): 730-732, 2024 Apr.

Article in En | MEDLINE | ID: mdl-38600188

Subject(s)

Autistic Disorder; Long QT Syndrome; Syndactyly; Humans; Autistic Disorder/genetics; Autistic Disorder/drug therapy; Autistic Disorder/therapy; Long QT Syndrome/genetics; Long QT Syndrome/drug therapy; Animals; Mice; Molecular Targeted Therapy

Key words

Autism spectrum disorders; Gene therapy; Stem cells; Therapeutics

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Full text: 1 Collection: 01-internacional Database: MEDLINE Main subject: Autistic Disorder / Long QT Syndrome / Syndactyly Limits: Animals / Humans Language: En Journal: Nature / Nature (Lond.) / Nature (London) Year: 2024 Document type: Article

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