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Genetic medicines for CF: Hype versus reality.
Alton, Eric W F W; Boyd, A Christopher; Davies, Jane C; Gill, Deborah R; Griesenbach, Uta; Harrison, Patrick T; Henig, Noreen; Higgins, Tracy; Hyde, Stephen C; Innes, J Alastair; Korman, Michael S D.
Afiliação
  • Alton EW; UK Cystic Fibrosis Gene Therapy Consortium, Edinburgh, Oxford, London.
  • Boyd AC; UK Cystic Fibrosis Gene Therapy Consortium, Edinburgh, Oxford, London.
  • Davies JC; UK Cystic Fibrosis Gene Therapy Consortium, Edinburgh, Oxford, London.
  • Gill DR; UK Cystic Fibrosis Gene Therapy Consortium, Edinburgh, Oxford, London.
  • Griesenbach U; UK Cystic Fibrosis Gene Therapy Consortium, Edinburgh, Oxford, London. u.griesenbach@imperial.ac.uk.
  • Harrison PT; Department of Physiology and BioSciences Institute, University College Cork, Cork, Ireland.
  • Henig N; ProQR Therapeutics NV, Leiden, The Netherlands.
  • Higgins T; UK Cystic Fibrosis Gene Therapy Consortium, Edinburgh, Oxford, London.
  • Hyde SC; UK Cystic Fibrosis Gene Therapy Consortium, Edinburgh, Oxford, London.
  • Innes JA; UK Cystic Fibrosis Gene Therapy Consortium, Edinburgh, Oxford, London.
  • Korman MS; Department of Pediatrics I - Pediatric Infectiology and Immunology - Translational Genomics and Gene Therapy, University of Tübingen, Tübingen, Germany.
Pediatr Pulmonol ; 51(S44): S5-S17, 2016 Oct.
Article em En | MEDLINE | ID: mdl-27662105

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Pediatr Pulmonol Ano de publicação: 2016 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Pediatr Pulmonol Ano de publicação: 2016 Tipo de documento: Article