Your browser doesn't support javascript.
loading
Selection-free genome editing of the sickle mutation in human adult hematopoietic stem/progenitor cells.
DeWitt, Mark A; Magis, Wendy; Bray, Nicolas L; Wang, Tianjiao; Berman, Jennifer R; Urbinati, Fabrizia; Heo, Seok-Jin; Mitros, Therese; Muñoz, Denise P; Boffelli, Dario; Kohn, Donald B; Walters, Mark C; Carroll, Dana; Martin, David I K; Corn, Jacob E.
Afiliação
  • DeWitt MA; Innovative Genomics Initiative, University of California, Berkeley, Berkeley, CA 94720, USA. Department of Molecular and Cellular Biology, University of California, Berkeley, Berkeley, CA 94720, USA.
  • Magis W; Children's Hospital Oakland Research Institute, University of California San Francisco (UCSF) Benioff Children's Hospital, Oakland, CA 94609, USA.
  • Bray NL; Innovative Genomics Initiative, University of California, Berkeley, Berkeley, CA 94720, USA. Department of Molecular and Cellular Biology, University of California, Berkeley, Berkeley, CA 94720, USA.
  • Wang T; Innovative Genomics Initiative, University of California, Berkeley, Berkeley, CA 94720, USA. Department of Molecular and Cellular Biology, University of California, Berkeley, Berkeley, CA 94720, USA.
  • Berman JR; Digital Biology Center, Bio-Rad Laboratories, Pleasanton, CA 94588, USA.
  • Urbinati F; Departments of Microbiology, Immunology, and Molecular Genetics; Pediatrics; and Molecular and Medical Pharmacology, University of California, Los Angeles, Los Angeles, CA 90095, USA.
  • Heo SJ; Children's Hospital Oakland Research Institute, University of California San Francisco (UCSF) Benioff Children's Hospital, Oakland, CA 94609, USA.
  • Mitros T; Department of Molecular and Cellular Biology, University of California, Berkeley, Berkeley, CA 94720, USA.
  • Muñoz DP; Children's Hospital Oakland Research Institute, University of California San Francisco (UCSF) Benioff Children's Hospital, Oakland, CA 94609, USA.
  • Boffelli D; Children's Hospital Oakland Research Institute, University of California San Francisco (UCSF) Benioff Children's Hospital, Oakland, CA 94609, USA.
  • Kohn DB; Departments of Microbiology, Immunology, and Molecular Genetics; Pediatrics; and Molecular and Medical Pharmacology, University of California, Los Angeles, Los Angeles, CA 90095, USA.
  • Walters MC; Children's Hospital Oakland Research Institute, University of California San Francisco (UCSF) Benioff Children's Hospital, Oakland, CA 94609, USA. Blood and Marrow Transplant Program, Division of Hematology, UCSF Benioff Children's Hospital, Oakland, CA 94609, USA.
  • Carroll D; Innovative Genomics Initiative, University of California, Berkeley, Berkeley, CA 94720, USA. Department of Biochemistry, University of Utah School of Medicine, Salt Lake City, UT 84112, USA. jcorn@berkeley.edu dimartin@chori.org dana@biochem.utah.edu.
  • Martin DI; Children's Hospital Oakland Research Institute, University of California San Francisco (UCSF) Benioff Children's Hospital, Oakland, CA 94609, USA. jcorn@berkeley.edu dimartin@chori.org dana@biochem.utah.edu.
  • Corn JE; Innovative Genomics Initiative, University of California, Berkeley, Berkeley, CA 94720, USA. Department of Molecular and Cellular Biology, University of California, Berkeley, Berkeley, CA 94720, USA. jcorn@berkeley.edu dimartin@chori.org dana@biochem.utah.edu.
Sci Transl Med ; 8(360): 360ra134, 2016 10 12.
Article em En | MEDLINE | ID: mdl-27733558

Texto completo: 1 Coleções: 01-internacional Contexto em Saúde: 1_ASSA2030 Base de dados: MEDLINE Assunto principal: Hemoglobina Falciforme / Células-Tronco Hematopoéticas / Células-Tronco Adultas / Edição de Genes / Anemia Falciforme Limite: Adult / Animals / Humans Idioma: En Revista: Sci Transl Med Ano de publicação: 2016 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Contexto em Saúde: 1_ASSA2030 Base de dados: MEDLINE Assunto principal: Hemoglobina Falciforme / Células-Tronco Hematopoéticas / Células-Tronco Adultas / Edição de Genes / Anemia Falciforme Limite: Adult / Animals / Humans Idioma: En Revista: Sci Transl Med Ano de publicação: 2016 Tipo de documento: Article