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Nonclinical Pharmacology/Toxicology Study of AAV8.TBG.mLDLR and AAV8.TBG.hLDLR in a Mouse Model of Homozygous Familial Hypercholesterolemia.
Greig, Jenny A; Limberis, Maria P; Bell, Peter; Chen, Shu-Jen; Calcedo, Roberto; Rader, Daniel J; Wilson, James M.
Afiliação
  • Greig JA; 1 Gene Therapy Program, Department of Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Limberis MP; 2 Department of Pathology and Laboratory Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Bell P; 1 Gene Therapy Program, Department of Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Chen SJ; 1 Gene Therapy Program, Department of Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Calcedo R; 1 Gene Therapy Program, Department of Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Rader DJ; 3 Division of Translational Medicine and Human Genetics, Department of Medicine, University of Pennsylvania , Philadelphia, Pennsylvania.
  • Wilson JM; 4 Department of Genetics, University of Pennsylvania , Philadelphia, Pennsylvania.
Hum Gene Ther Clin Dev ; 28(1): 28-38, 2017 03.
Article em En | MEDLINE | ID: mdl-28319445

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Receptores de LDL / Terapia Genética / Dependovirus / Desaminase APOBEC-1 / Vetores Genéticos / Hiperlipoproteinemia Tipo II / Fígado Limite: Animals / Female / Humans / Male Idioma: En Revista: Hum Gene Ther Clin Dev Ano de publicação: 2017 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Receptores de LDL / Terapia Genética / Dependovirus / Desaminase APOBEC-1 / Vetores Genéticos / Hiperlipoproteinemia Tipo II / Fígado Limite: Animals / Female / Humans / Male Idioma: En Revista: Hum Gene Ther Clin Dev Ano de publicação: 2017 Tipo de documento: Article