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Chaperone effect of sulfated disaccharide from heparin on mutant iduronate-2-sulfatase in mucopolysaccharidosis type II.
Hoshina, Hiroo; Shimada, Yohta; Higuchi, Takashi; Kobayashi, Hiroshi; Ida, Hiroyuki; Ohashi, Toya.
Afiliação
  • Hoshina H; Division of Gene Therapy, Research Center for Medical Sciences, The Jikei University School of Medicine, Tokyo 105-8461, Japan; Department of Pediatrics, The Jikei University School of Medicine, Tokyo 105-8461, Japan.
  • Shimada Y; Division of Gene Therapy, Research Center for Medical Sciences, The Jikei University School of Medicine, Tokyo 105-8461, Japan. Electronic address: shimada_y@jikei.ac.jp.
  • Higuchi T; Division of Gene Therapy, Research Center for Medical Sciences, The Jikei University School of Medicine, Tokyo 105-8461, Japan.
  • Kobayashi H; Division of Gene Therapy, Research Center for Medical Sciences, The Jikei University School of Medicine, Tokyo 105-8461, Japan; Department of Pediatrics, The Jikei University School of Medicine, Tokyo 105-8461, Japan.
  • Ida H; Division of Gene Therapy, Research Center for Medical Sciences, The Jikei University School of Medicine, Tokyo 105-8461, Japan; Department of Pediatrics, The Jikei University School of Medicine, Tokyo 105-8461, Japan.
  • Ohashi T; Division of Gene Therapy, Research Center for Medical Sciences, The Jikei University School of Medicine, Tokyo 105-8461, Japan; Department of Pediatrics, The Jikei University School of Medicine, Tokyo 105-8461, Japan.
Mol Genet Metab ; 123(2): 118-122, 2018 02.
Article em En | MEDLINE | ID: mdl-29289480

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Sulfatos / Regulação Enzimológica da Expressão Gênica / Mucopolissacaridose II / Chaperonas Moleculares / Dissacarídeos / Iduronato Sulfatase / Mutação Limite: Humans Idioma: En Revista: Mol Genet Metab Ano de publicação: 2018 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Sulfatos / Regulação Enzimológica da Expressão Gênica / Mucopolissacaridose II / Chaperonas Moleculares / Dissacarídeos / Iduronato Sulfatase / Mutação Limite: Humans Idioma: En Revista: Mol Genet Metab Ano de publicação: 2018 Tipo de documento: Article