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T cell dynamics and response of the microbiota after gene therapy to treat X-linked severe combined immunodeficiency.
Clarke, Erik L; Connell, A Jesse; Six, Emmanuelle; Kadry, Nadia A; Abbas, Arwa A; Hwang, Young; Everett, John K; Hofstaedter, Casey E; Marsh, Rebecca; Armant, Myriam; Kelsen, Judith; Notarangelo, Luigi D; Collman, Ronald G; Hacein-Bey-Abina, Salima; Kohn, Donald B; Cavazzana, Marina; Fischer, Alain; Williams, David A; Pai, Sung-Yun; Bushman, Frederic D.
Afiliação
  • Clarke EL; Department of Microbiology, University of Pennsylvania School of Medicine, 3610 Hamilton Walk, Philadelphia, PA, 19104-6076, USA.
  • Connell AJ; Department of Microbiology, University of Pennsylvania School of Medicine, 3610 Hamilton Walk, Philadelphia, PA, 19104-6076, USA.
  • Six E; Imagine Institute, Paris Descartes-Sorbonne Paris Cité University, Paris, France.
  • Kadry NA; Laboratory of Human Lymphohematopoiesis, INSERM UMR 1163, Paris, France.
  • Abbas AA; Department of Microbiology, University of Pennsylvania School of Medicine, 3610 Hamilton Walk, Philadelphia, PA, 19104-6076, USA.
  • Hwang Y; Department of Microbiology, University of Pennsylvania School of Medicine, 3610 Hamilton Walk, Philadelphia, PA, 19104-6076, USA.
  • Everett JK; Department of Microbiology, University of Pennsylvania School of Medicine, 3610 Hamilton Walk, Philadelphia, PA, 19104-6076, USA.
  • Hofstaedter CE; Department of Microbiology, University of Pennsylvania School of Medicine, 3610 Hamilton Walk, Philadelphia, PA, 19104-6076, USA.
  • Marsh R; Division of Gastroenterology, Hepatology, and Nutrition, The Children's Hospital of Philadelphia, Philadelphia, PA, USA.
  • Armant M; Cincinnati Children's Hospital Medical Center, 3333 Burnet Avenue, Cincinnati, OH, 45229-3039, USA.
  • Kelsen J; Boston Children's Hospital, Karp 08125.3, 300 Longwood Avenue, Boston, MA, 02115, USA.
  • Notarangelo LD; Division of Gastroenterology, Hepatology, and Nutrition, The Children's Hospital of Philadelphia, Philadelphia, PA, USA.
  • Collman RG; Laboratory of Host Defenses, Laboratory of Clinical Infectious Diseases, Immune Deficiency Genetics Section, NIAID, NIH, Bethesda, MD, USA.
  • Hacein-Bey-Abina S; Department of Medicine, University of Pennsylvania School of Medicine, 3610 Hamilton Walk, Philadelphia, PA, 19104-6076, USA.
  • Kohn DB; Clinical Immunology Laboratory, Groupe Hospitalier Universitaire Paris-Sud, Hôpital Kremlin-Bicêtre, Assistance Publique-Hôpitaux de Paris, 78, r. du Général-Leclerc, 94270, Le-Kremlin-Bicêtre, France.
  • Cavazzana M; UTCBS CNRS UMR 8258, INSERM U1022, Faculté de Pharmacie de Paris, Université Paris Descartes, Sorbonne Paris Cité, Chimie Paris-Tech, 4 av. de l'observatoire, 75006, Paris, France.
  • Fischer A; Departments of Microbiology, Immunology & Molecular Genetics; and Pediatrics, University of California, Los Angeles, USA.
  • Williams DA; Imagine Institute, Paris Descartes-Sorbonne Paris Cité University, Paris, France.
  • Pai SY; Laboratory of Human Lymphohematopoiesis, INSERM UMR 1163, Paris, France.
  • Bushman FD; Biotherapy Department, Necker Children's Hospital, Assistance Publique-Hôpitaux de Paris, Paris, France.
Genome Med ; 10(1): 70, 2018 09 28.
Article em En | MEDLINE | ID: mdl-30261899

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Linfócitos T / Terapia Genética / Doenças por Imunodeficiência Combinada Ligada ao Cromossomo X / Microbiota Limite: Child, preschool / Humans Idioma: En Revista: Genome Med Ano de publicação: 2018 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Linfócitos T / Terapia Genética / Doenças por Imunodeficiência Combinada Ligada ao Cromossomo X / Microbiota Limite: Child, preschool / Humans Idioma: En Revista: Genome Med Ano de publicação: 2018 Tipo de documento: Article