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Liver Expression of a MiniATP7B Gene Results in Long-Term Restoration of Copper Homeostasis in a Wilson Disease Model in Mice.
Murillo, Oihana; Moreno, Daniel; Gazquez, Cristina; Barberia, Miren; Cenzano, Itziar; Navarro, Iñigo; Uriarte, Iker; Sebastian, Victor; Arruebo, Manuel; Ferrer, Veronica; Bénichou, Bernard; Combal, Jean Philippe; Prieto, Jesus; Hernandez-Alcoceba, Ruben; Gonzalez Aseguinolaza, Gloria.
Afiliação
  • Murillo O; Gene Therapy and Regulation of Gene Expression Program, CIMA, FIMA, University of Navarra, Navarra Institute for Health Research (IdisNA), Pamplona, Spain.
  • Moreno D; Gene Therapy and Regulation of Gene Expression Program, CIMA, FIMA, University of Navarra, Navarra Institute for Health Research (IdisNA), Pamplona, Spain.
  • Gazquez C; Gene Therapy and Regulation of Gene Expression Program, CIMA, FIMA, University of Navarra, Navarra Institute for Health Research (IdisNA), Pamplona, Spain.
  • Barberia M; Gene Therapy and Regulation of Gene Expression Program, CIMA, FIMA, University of Navarra, Navarra Institute for Health Research (IdisNA), Pamplona, Spain.
  • Cenzano I; Gene Therapy and Regulation of Gene Expression Program, CIMA, FIMA, University of Navarra, Navarra Institute for Health Research (IdisNA), Pamplona, Spain.
  • Navarro I; Department of Chemistry and Soil Sciences, University of Navarra, IdisNA, Pamplona, Spain.
  • Uriarte I; Hepatology Program, CIMA, FIMA, University of Navarra, IdisNA, Pamplona, Spain.
  • Sebastian V; CIBERehd, Instituto de Salud Carlos III, Clinica Universidad de Navarra, Pamplona, Spain.
  • Arruebo M; Department of Chemical Engineering, Aragón Institute of Nanoscience (INA), University of Zaragoza, and Aragon Health Research Institute (IIS Aragon), Zaragoza, Spain.
  • Ferrer V; Networking Research Center on Bioengineering, Biomaterials and Nanomedicine, CIBER-BBN, 28029-, Madrid, Spain.
  • Bénichou B; Department of Chemical Engineering, Aragón Institute of Nanoscience (INA), University of Zaragoza, and Aragon Health Research Institute (IIS Aragon), Zaragoza, Spain.
  • Combal JP; Networking Research Center on Bioengineering, Biomaterials and Nanomedicine, CIBER-BBN, 28029-, Madrid, Spain.
  • Prieto J; Vivet Therapeutics SAS, Paris, France.
  • Hernandez-Alcoceba R; Vivet Therapeutics SAS, Paris, France.
  • Gonzalez Aseguinolaza G; Vivet Therapeutics SAS, Paris, France.
Hepatology ; 70(1): 108-126, 2019 07.
Article em En | MEDLINE | ID: mdl-30706949

Texto completo: 1 Coleções: 01-internacional Contexto em Saúde: 6_ODS3_enfermedades_notrasmisibles Base de dados: MEDLINE Assunto principal: Terapia Genética / Cobre / ATPases Transportadoras de Cobre / Degeneração Hepatolenticular Tipo de estudo: Evaluation_studies Limite: Animals Idioma: En Revista: Hepatology Ano de publicação: 2019 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Contexto em Saúde: 6_ODS3_enfermedades_notrasmisibles Base de dados: MEDLINE Assunto principal: Terapia Genética / Cobre / ATPases Transportadoras de Cobre / Degeneração Hepatolenticular Tipo de estudo: Evaluation_studies Limite: Animals Idioma: En Revista: Hepatology Ano de publicação: 2019 Tipo de documento: Article