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mRNA as a Novel Treatment Strategy for Hereditary Spastic Paraplegia Type 5.
Hauser, Stefan; Poenisch, Marion; Schelling, Yvonne; Höflinger, Philip; Schuster, Stefanie; Teegler, Axel; Betten, Rabea; Gustafsson, Jan-Åke; Hübener-Schmid, Jeannette; Schlake, Thomas; Chevessier-Tünnesen, Frédéric; Horscroft, Nigel; Björkhem, Ingemar; Schöls, Ludger.
Afiliação
  • Hauser S; German Center for Neurodegenerative Diseases (DZNE), 72076 Tübingen, Germany.
  • Poenisch M; Department of Neurology and Hertie Institute for Clinical Brain Research, University of Tübingen, 72076 Tübingen, Germany.
  • Schelling Y; CureVac AG, Paul-Ehrlich-Strasse 15, 72076 Tübingen, Germany.
  • Höflinger P; German Center for Neurodegenerative Diseases (DZNE), 72076 Tübingen, Germany.
  • Schuster S; Department of Neurology and Hertie Institute for Clinical Brain Research, University of Tübingen, 72076 Tübingen, Germany.
  • Teegler A; German Center for Neurodegenerative Diseases (DZNE), 72076 Tübingen, Germany.
  • Betten R; Department of Neurology and Hertie Institute for Clinical Brain Research, University of Tübingen, 72076 Tübingen, Germany.
  • Gustafsson JÅ; Graduate School of Cellular and Molecular Neuroscience, University of Tübingen, 72076 Tübingen, Germany.
  • Hübener-Schmid J; German Center for Neurodegenerative Diseases (DZNE), 72076 Tübingen, Germany.
  • Schlake T; Department of Neurology and Hertie Institute for Clinical Brain Research, University of Tübingen, 72076 Tübingen, Germany.
  • Chevessier-Tünnesen F; Graduate School of Cellular and Molecular Neuroscience, University of Tübingen, 72076 Tübingen, Germany.
  • Horscroft N; CureVac AG, Paul-Ehrlich-Strasse 15, 72076 Tübingen, Germany.
  • Björkhem I; CureVac AG, Paul-Ehrlich-Strasse 15, 72076 Tübingen, Germany.
  • Schöls L; Department of Biosciences and Nutrition, Center for Innovative Medicine, Karolinska Institutet, 141 83 Huddinge, Sweden.
Mol Ther Methods Clin Dev ; 15: 359-370, 2019 Dec 13.
Article em En | MEDLINE | ID: mdl-31828178

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Methods Clin Dev Ano de publicação: 2019 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Methods Clin Dev Ano de publicação: 2019 Tipo de documento: Article