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Targeting Repeated Regions Unique to a Gene Is an Effective Strategy for Discovering Potent and Efficacious Antisense Oligonucleotides.
Pedersen, Lykke; Hagedorn, Peter; Vikeså, Jonas; Karlsen, Signe Tang; Særmark, Pia; Koch, Troels; Lindow, Morten.
Afiliação
  • Pedersen L; Therapeutic Modalities, Roche Pharma Research and Early Development, Roche Innovation Center Copenhagen, 2970 Hørsholm, Denmark. Electronic address: lykke.pedersen@roche.com.
  • Hagedorn P; Therapeutic Modalities, Roche Pharma Research and Early Development, Roche Innovation Center Copenhagen, 2970 Hørsholm, Denmark.
  • Vikeså J; Therapeutic Modalities, Roche Pharma Research and Early Development, Roche Innovation Center Copenhagen, 2970 Hørsholm, Denmark.
  • Karlsen ST; The Bioinformatics Centre, Department of Biology, University of Copenhagen, 2100 Copenhagen, Denmark.
  • Særmark P; The Bioinformatics Centre, Department of Biology, University of Copenhagen, 2100 Copenhagen, Denmark.
  • Koch T; Therapeutic Modalities, Roche Pharma Research and Early Development, Roche Innovation Center Copenhagen, 2970 Hørsholm, Denmark.
  • Lindow M; Therapeutic Modalities, Roche Pharma Research and Early Development, Roche Innovation Center Copenhagen, 2970 Hørsholm, Denmark.
Mol Ther Nucleic Acids ; 19: 124-131, 2020 Mar 06.
Article em En | MEDLINE | ID: mdl-31846799

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Ano de publicação: 2020 Tipo de documento: Article