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Single AAV-mediated mutation replacement genome editing in limited number of photoreceptors restores vision in mice.
Nishiguchi, Koji M; Fujita, Kosuke; Miya, Fuyuki; Katayama, Shota; Nakazawa, Toru.
Afiliação
  • Nishiguchi KM; Department of Advanced Ophthalmic Medicine, Tohoku University Graduate School of Medicine, Sendai, 980-8574, Japan. nishiguchi@oph.med.tohoku.ac.jp.
  • Fujita K; Department of Ophthalmology, Tohoku University Graduate School of Medicine, Sendai, 980-8574, Japan. nishiguchi@oph.med.tohoku.ac.jp.
  • Miya F; Department of Ophthalmic Imaging and Information Analytics, Tohoku University Graduate School of Medicine, Sendai, 980-8574, Japan.
  • Katayama S; Department of Medical Science Mathematics, Medical Research Institute, Tokyo Medical and Dental University, Tokyo, 113-8510, Japan.
  • Nakazawa T; Department of Advanced Ophthalmic Medicine, Tohoku University Graduate School of Medicine, Sendai, 980-8574, Japan.
Nat Commun ; 11(1): 482, 2020 01 24.
Article em En | MEDLINE | ID: mdl-31980606

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Dependovirus / Células Fotorreceptoras de Vertebrados / Distrofias Retinianas / Edição de Genes Tipo de estudo: Clinical_trials Limite: Animals / Humans Idioma: En Revista: Nat Commun Ano de publicação: 2020 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Dependovirus / Células Fotorreceptoras de Vertebrados / Distrofias Retinianas / Edição de Genes Tipo de estudo: Clinical_trials Limite: Animals / Humans Idioma: En Revista: Nat Commun Ano de publicação: 2020 Tipo de documento: Article