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Intra-cisterna magna delivery of an AAV vector with the GLUT1 promoter in a pig recapitulates the physiological expression of SLC2A1.
Nakamura, Sachie; Osaka, Hitoshi; Muramatsu, Shin-Ichi; Takino, Naomi; Ito, Mika; Jimbo, Eriko F; Watanabe, Chika; Hishikawa, Shuji; Nakajima, Takeshi; Yamagata, Takanori.
Afiliação
  • Nakamura S; Department of Pediatrics, Jichi Medical University, Tochigi, Japan.
  • Osaka H; Department of Pediatrics, Jichi Medical University, Tochigi, Japan. hosaka@jichi.ac.jp.
  • Muramatsu SI; Division of Neurological Gene Therapy, Jichi Medical University, Tochigi, Japan.
  • Takino N; Center for Gene and Cell Therapy, The Institute of Medical Science, The University of Tokyo, Bunkyo City, Tokyo, Japan.
  • Ito M; Division of Neurological Gene Therapy, Jichi Medical University, Tochigi, Japan.
  • Jimbo EF; Division of Neurological Gene Therapy, Jichi Medical University, Tochigi, Japan.
  • Watanabe C; Department of Pediatrics, Jichi Medical University, Tochigi, Japan.
  • Hishikawa S; Department of Pediatrics, Jichi Medical University, Tochigi, Japan.
  • Nakajima T; Center for Development of Advanced Medical Technology, Jichi Medical University, Tochigi, Japan.
  • Yamagata T; Department of Neurosurgery, Jichi Medical University, Tochigi, Japan.
Gene Ther ; 28(6): 329-338, 2021 06.
Article em En | MEDLINE | ID: mdl-33077933

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Cisterna Magna / Dependovirus Limite: Animals Idioma: En Revista: Gene Ther Ano de publicação: 2021 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Cisterna Magna / Dependovirus Limite: Animals Idioma: En Revista: Gene Ther Ano de publicação: 2021 Tipo de documento: Article