Your browser doesn't support javascript.
loading
Treatment of GM2 Gangliosidosis in Adult Sandhoff Mice Using an Intravenous Self-Complementary Hexosaminidase Vector.
Osmon, Karlaina Jl; Thompson, Patrick; Woodley, Evan; Karumuthil-Melethil, Subha; Heindel, Cliff; Keimel, John G; Kaemmerer, William F; Gray, Steven J; Walia, Jagdeep S.
Afiliação
  • Osmon KJ; Centre for Neuroscience Studies, Queen\'s University, Kingston, ON K7L 3N6, Canada.
  • Thompson P; Department of Biomedical and Molecular Sciences, Queen\'s University, Kingston, ON K7L 3N6, Canada.
  • Woodley E; Medical Genetics/Departments of Pediatrics, Queen\'s University, Kingston, ON K7L 2V7, Canada.
  • Karumuthil-Melethil S; Department of Biomedical and Molecular Sciences, Queen\'s University, Kingston, ON K7L 3N6, Canada.
  • Heindel C; Gene Therapy Center, University of North Carolina, Chapel Hill, NC, USA.
  • Keimel JG; Gene Therapy Center, University of North Carolina, Chapel Hill, NC, USA.
  • Kaemmerer WF; New Hope Research Foundation, North Oaks, MN, USA.
  • Gray SJ; New Hope Research Foundation, North Oaks, MN, USA.
  • Walia JS; Gene Therapy Center, University of North Carolina, Chapel Hill, NC, USA.
Curr Gene Ther ; 22(3): 262-276, 2022.
Article em En | MEDLINE | ID: mdl-34530708

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Doença de Sandhoff / Gangliosidoses GM2 Limite: Animals / Humans Idioma: En Revista: Curr Gene Ther Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Doença de Sandhoff / Gangliosidoses GM2 Limite: Animals / Humans Idioma: En Revista: Curr Gene Ther Ano de publicação: 2022 Tipo de documento: Article