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Infigratinib in children with achondroplasia: the PROPEL and PROPEL 2 studies.
Savarirayan, Ravi; De Bergua, Josep Maria; Arundel, Paul; McDevitt, Helen; Cormier-Daire, Valerie; Saraff, Vrinda; Skae, Mars; Delgado, Borja; Leiva-Gea, Antonio; Santos-Simarro, Fernando; Salles, Jean Pierre; Nicolino, Marc; Rossi, Massimiliano; Kannu, Peter; Bober, Michael B; Phillips, John; Saal, Howard; Harmatz, Paul; Burren, Christine; Gotway, Garrett; Cho, Terry; Muslimova, Elena; Weng, Richard; Rogoff, Daniela; Hoover-Fong, Julie; Irving, Melita.
Afiliação
  • Savarirayan R; Murdoch Children's Research Institute, Parkville, VIC 3052, Australia.
  • De Bergua JM; Unidad de Cirugía Artroscópica (UCA), Hospital Vithas Vitoria, Vitoria-Gasteiz, Spain.
  • Arundel P; Sheffield Children's NHS Foundation Trust, Sheffield, UK.
  • McDevitt H; NHS Greater Glasgow and Clyde, Glasgow, UK.
  • Cormier-Daire V; Imagine Institute, Hôpital Necker-Enfants Malades, University of Paris, Paris, France.
  • Saraff V; Birmingham Women's and Children's NHS Foundation Trust, Birmingham, UK.
  • Skae M; Manchester University NHS Foundation Trust, The University of Manchester, Manchester, UK.
  • Delgado B; Campus de Teatinos sin número, Malaga, Spain.
  • Leiva-Gea A; Instituto de Investigación Biomédica de Málaga (IBIMA), Malaga, Spain.
  • Santos-Simarro F; Instituto de Genética Médica y Molecular (INGEMM), Unidad Multidisciplinar de Displasias Esqueléticas (UMDE), Hospital Universitario La Paz, Instituto de Investigación del Hospital Universitario La Paz (IdiPAZ), Centro de Investigación Biomédica en Red de enfermedades raras (CIBERER), Instituto de S
  • Salles JP; Hôpital des Enfants, Toulouse, France.
  • Nicolino M; Hôpital Femme Mère Enfant, Hospices Civils de Lyon, France.
  • Rossi M; Lyon University Hospital, Bron, France.
  • Kannu P; Stollery Children's Hospital, University of Alberta, Edmonton, AB, Canada.
  • Bober MB; Nemours Children's Hospital, Wilmington, DE, USA.
  • Phillips J; Vanderbilt University Medical Center, Nashville, TN, USA.
  • Saal H; Cincinnati Children's Hospital Medical Center, Cincinnati, OH, USA.
  • Harmatz P; UCSF Benioff Children's Hospital Oakland, Oakland, CA, USA.
  • Burren C; University Hospitals Bristol and Weston NHS Foundation Trust, Bristol, UK.
  • Gotway G; Children's Medical Center Dallas, Texas, TX, USA.
  • Cho T; QED Therapeutics Inc., San Francisco, CA, USA.
  • Muslimova E; QED Therapeutics Inc., San Francisco, CA, USA.
  • Weng R; QED Therapeutics Inc., San Francisco, CA, USA.
  • Rogoff D; QED Therapeutics Inc., San Francisco, CA, USA.
  • Hoover-Fong J; School of Medicine, Johns Hopkins University, Baltimore, MA, USA.
  • Irving M; Guy's and Saint Thomas' NHS Foundation Trust, London, UK.
Ther Adv Musculoskelet Dis ; 14: 1759720X221084848, 2022.
Article em En | MEDLINE | ID: mdl-35342457

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Guideline / Prognostic_studies / Qualitative_research Aspecto: Ethics Idioma: En Revista: Ther Adv Musculoskelet Dis Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Guideline / Prognostic_studies / Qualitative_research Aspecto: Ethics Idioma: En Revista: Ther Adv Musculoskelet Dis Ano de publicação: 2022 Tipo de documento: Article