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Nedosiran, a Candidate siRNA Drug for the Treatment of Primary Hyperoxaluria: Design, Development, and Clinical Studies.
Liu, Anna; Zhao, Jenny; Shah, Milan; Migliorati, Julia M; Tawfik, Sherouk M; Bahal, Raman; Rasmussen, Theodore P; Manautou, Jose E; Zhong, Xiao-Bo.
Afiliação
  • Liu A; Department of Pharmaceutical Sciences, School of Pharmacy, University of Connecticut, Storrs, Connecticut06269, United States.
  • Zhao J; Department of Pharmaceutical Sciences, School of Pharmacy, University of Connecticut, Storrs, Connecticut06269, United States.
  • Shah M; Department of Pharmaceutical Sciences, School of Pharmacy, University of Connecticut, Storrs, Connecticut06269, United States.
  • Migliorati JM; Department of Pharmaceutical Sciences, School of Pharmacy, University of Connecticut, Storrs, Connecticut06269, United States.
  • Tawfik SM; Department of Pharmaceutical Sciences, School of Pharmacy, University of Connecticut, Storrs, Connecticut06269, United States.
  • Bahal R; Department of Pharmaceutical Sciences, School of Pharmacy, University of Connecticut, Storrs, Connecticut06269, United States.
  • Rasmussen TP; Department of Pharmaceutical Sciences, School of Pharmacy, University of Connecticut, Storrs, Connecticut06269, United States.
  • Manautou JE; Department of Pharmaceutical Sciences, School of Pharmacy, University of Connecticut, Storrs, Connecticut06269, United States.
  • Zhong XB; Department of Pharmaceutical Sciences, School of Pharmacy, University of Connecticut, Storrs, Connecticut06269, United States.
ACS Pharmacol Transl Sci ; 5(11): 1007-1016, 2022 Nov 11.
Article em En | MEDLINE | ID: mdl-36407951

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: ACS Pharmacol Transl Sci Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: ACS Pharmacol Transl Sci Ano de publicação: 2022 Tipo de documento: Article