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Histone deacetylase inhibitors improve antisense-mediated exon-skipping efficacy in mdx mice.
Bizot, Flavien; Goossens, Remko; Tensorer, Thomas; Dmitriev, Sergei; Garcia, Luis; Aartsma-Rus, Annemieke; Spitali, Pietro; Goyenvalle, Aurélie.
Afiliação
  • Bizot F; Université Paris-Saclay, UVSQ, Inserm, END-ICAP, 78000 Versailles, France.
  • Goossens R; Department of Human Genetics, Leiden University Medical Center, 2333 ZA Leiden, the Netherlands.
  • Tensorer T; SQY Therapeutics, UVSQ, END-ICAP, 78180 Montigny le Bretonneux, France.
  • Dmitriev S; SQY Therapeutics, UVSQ, END-ICAP, 78180 Montigny le Bretonneux, France.
  • Garcia L; Université Paris-Saclay, UVSQ, Inserm, END-ICAP, 78000 Versailles, France.
  • Aartsma-Rus A; Department of Human Genetics, Leiden University Medical Center, 2333 ZA Leiden, the Netherlands.
  • Spitali P; Department of Human Genetics, Leiden University Medical Center, 2333 ZA Leiden, the Netherlands.
  • Goyenvalle A; Université Paris-Saclay, UVSQ, Inserm, END-ICAP, 78000 Versailles, France.
Mol Ther Nucleic Acids ; 30: 606-620, 2022 Dec 13.
Article em En | MEDLINE | ID: mdl-36514350

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Ano de publicação: 2022 Tipo de documento: Article