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Challenges in Gene Therapy for Somatic Reverted Mosaicism in X-Linked Combined Immunodeficiency by CRISPR/Cas9 and Prime Editing.
Hou, Yujuan; Ureña-Bailén, Guillermo; Mohammadian Gol, Tahereh; Gratz, Paul Gerhard; Gratz, Hans Peter; Roig-Merino, Alicia; Antony, Justin S; Lamsfus-Calle, Andrés; Daniel-Moreno, Alberto; Handgretinger, Rupert; Mezger, Markus.
Afiliação
  • Hou Y; Department of Pediatrics I, Hematology and Oncology, University Children's Hospital, University of Tübingen, 72076 Tuebingen, Germany.
  • Ureña-Bailén G; Department of Pediatrics I, Hematology and Oncology, University Children's Hospital, University of Tübingen, 72076 Tuebingen, Germany.
  • Mohammadian Gol T; Department of Pediatrics I, Hematology and Oncology, University Children's Hospital, University of Tübingen, 72076 Tuebingen, Germany.
  • Gratz PG; Department of Pediatrics I, Hematology and Oncology, University Children's Hospital, University of Tübingen, 72076 Tuebingen, Germany.
  • Gratz HP; Department of Pediatrics I, Hematology and Oncology, University Children's Hospital, University of Tübingen, 72076 Tuebingen, Germany.
  • Roig-Merino A; MaxCyte Inc., Rockville, MD 20850, USA.
  • Antony JS; Department of Pediatrics I, Hematology and Oncology, University Children's Hospital, University of Tübingen, 72076 Tuebingen, Germany.
  • Lamsfus-Calle A; Department of Pediatrics I, Hematology and Oncology, University Children's Hospital, University of Tübingen, 72076 Tuebingen, Germany.
  • Daniel-Moreno A; Department of Pediatrics I, Hematology and Oncology, University Children's Hospital, University of Tübingen, 72076 Tuebingen, Germany.
  • Handgretinger R; Department of Pediatrics I, Hematology and Oncology, University Children's Hospital, University of Tübingen, 72076 Tuebingen, Germany.
  • Mezger M; Department of Pediatrics I, Hematology and Oncology, University Children's Hospital, University of Tübingen, 72076 Tuebingen, Germany.
Genes (Basel) ; 13(12)2022 12 13.
Article em En | MEDLINE | ID: mdl-36553615

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Doenças por Imunodeficiência Combinada Ligada ao Cromossomo X Limite: Humans Idioma: En Revista: Genes (Basel) Ano de publicação: 2022 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Doenças por Imunodeficiência Combinada Ligada ao Cromossomo X Limite: Humans Idioma: En Revista: Genes (Basel) Ano de publicação: 2022 Tipo de documento: Article