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Pathological modeling of glycogen storage disease type III with CRISPR/Cas9 edited human pluripotent stem cells.
Rossiaud, Lucille; Fragner, Pascal; Barbon, Elena; Gardin, Antoine; Benabides, Manon; Pellier, Emilie; Cosette, Jérémie; El Kassar, Lina; Giraud-Triboult, Karine; Nissan, Xavier; Ronzitti, Giuseppe; Hoch, Lucile.
Afiliação
  • Rossiaud L; CECS, I-Stem, Corbeil-Essonnes, France.
  • Fragner P; INSERM U861, I-Stem, Corbeil-Essonnes, France.
  • Barbon E; UEVE U861, I-Stem, Corbeil-Essonnes, France.
  • Gardin A; Genethon, Evry, France.
  • Benabides M; Université Paris-Saclay, Univ Evry, Inserm, Genethon, Integrare Research Unit UMR_S951, Evry, France.
  • Pellier E; CECS, I-Stem, Corbeil-Essonnes, France.
  • Cosette J; INSERM U861, I-Stem, Corbeil-Essonnes, France.
  • El Kassar L; UEVE U861, I-Stem, Corbeil-Essonnes, France.
  • Giraud-Triboult K; Genethon, Evry, France.
  • Nissan X; Université Paris-Saclay, Univ Evry, Inserm, Genethon, Integrare Research Unit UMR_S951, Evry, France.
  • Ronzitti G; Genethon, Evry, France.
  • Hoch L; Université Paris-Saclay, Univ Evry, Inserm, Genethon, Integrare Research Unit UMR_S951, Evry, France.
Front Cell Dev Biol ; 11: 1163427, 2023.
Article em En | MEDLINE | ID: mdl-37250895

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Front Cell Dev Biol Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Front Cell Dev Biol Ano de publicação: 2023 Tipo de documento: Article