AAV-vectored base editor <i>trans</i>-splicing delivers dystrophin repair.

Li, Zhen; Gonçalves, Manuel A F V

AAV-vectored base editor trans-splicing delivers dystrophin repair.

Li, Zhen; Gonçalves, Manuel A F V.

Afiliação

Li Z; Leiden University Medical Centre, Department of Cell and Chemical Biology, Einthovenweg 20, 2333 ZC Leiden, the Netherlands.
Gonçalves MAFV; Leiden University Medical Centre, Department of Cell and Chemical Biology, Einthovenweg 20, 2333 ZC Leiden, the Netherlands.

Mol Ther Nucleic Acids ; 32: 900-902, 2023 Jun 13.

Article em En | MEDLINE | ID: mdl-37346982

Texto completo

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10280080
https://dx.doi.org/10.1016/j.omtn.2023.05.013

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Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Ano de publicação: 2023 Tipo de documento: Article

Texto completo

https://www.ncbi.nlm.nih.gov/pmc/articles/PMC10280080
https://dx.doi.org/10.1016/j.omtn.2023.05.013

Imprimir

XML

PubMed Links

Buscar no Google

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Idioma: En Revista: Mol Ther Nucleic Acids Ano de publicação: 2023 Tipo de documento: Article