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Results of a phase 1/2 study of cemdisiran in healthy subjects and patients with paroxysmal nocturnal hemoglobinuria.
Gaya, Anna; Munir, Talha; Urbano-Ispizua, Alvaro; Griffin, Morag; Taubel, Jorg; Bush, Jim; Bhan, Ishir; Borodovsky, Anna; Wang, Yue; Badri, Prajakta; Garg, Pushkal.
Afiliação
  • Gaya A; Hospital Clinic of Barcelona Barcelona Spain.
  • Munir T; Leeds Teaching Hospitals St. James' University Hospital Leeds UK.
  • Urbano-Ispizua A; Hospital Clinic of Barcelona Barcelona Spain.
  • Griffin M; August Pi i Sunyer Biomedical Research Institute Barcelona Spain.
  • Taubel J; Leeds Teaching Hospitals St. James' University Hospital Leeds UK.
  • Bush J; Richmond Pharmacology, Ltd St. George's University of London London UK.
  • Bhan I; Labcorp Clinical Research Unit Springfield House, Hyde St Leeds UK.
  • Borodovsky A; Alnylam Pharmaceuticals Cambridge Massachusetts USA.
  • Wang Y; Alnylam Pharmaceuticals Cambridge Massachusetts USA.
  • Badri P; Alnylam Pharmaceuticals Cambridge Massachusetts USA.
  • Garg P; Alnylam Pharmaceuticals Cambridge Massachusetts USA.
EJHaem ; 4(3): 612-624, 2023 Aug.
Article em En | MEDLINE | ID: mdl-37601837

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Clinical_trials Idioma: En Revista: EJHaem Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Tipo de estudo: Clinical_trials Idioma: En Revista: EJHaem Ano de publicação: 2023 Tipo de documento: Article