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Emerging Gene Therapy Approaches in the Management of Spinal Muscular Atrophy (SMA): An Overview of Clinical Trials and Patent Landscape.
Ponomarev, Aleksei S; Chulpanova, Daria S; Yanygina, Lina M; Solovyeva, Valeriya V; Rizvanov, Albert A.
Afiliação
  • Ponomarev AS; Institute of Fundamental Medicine and Biology, Kazan Federal University, 420008 Kazan, Russia.
  • Chulpanova DS; Institute of Fundamental Medicine and Biology, Kazan Federal University, 420008 Kazan, Russia.
  • Yanygina LM; Institute of Fundamental Medicine and Biology, Kazan Federal University, 420008 Kazan, Russia.
  • Solovyeva VV; Institute of Fundamental Medicine and Biology, Kazan Federal University, 420008 Kazan, Russia.
  • Rizvanov AA; Institute of Fundamental Medicine and Biology, Kazan Federal University, 420008 Kazan, Russia.
Int J Mol Sci ; 24(18)2023 Sep 06.
Article em En | MEDLINE | ID: mdl-37762045

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Atrofia Muscular Espinal Limite: Humans Idioma: En Revista: Int J Mol Sci Ano de publicação: 2023 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Atrofia Muscular Espinal Limite: Humans Idioma: En Revista: Int J Mol Sci Ano de publicação: 2023 Tipo de documento: Article