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EAHAD haemophilia gene therapy clinical outcome database (EAHAD-GTD).
Miesbach, Wolfgang; Boban, Ana; Chowdary, Pratima; Coppens, Michiel; Crato, Miguel; Jimenez-Yuste, Victor; Klamroth, Robert; Makris, Mike; Mulders, Greta; Peyvandi, Flora.
Afiliação
  • Miesbach W; Medical Clinic 2, Institute of Transfusion Medicine, University Hospital Frankfurt, Frankfurt am Main, Germany.
  • Boban A; Department of Haematology, Haemophilia Centre, University Hospital Centre Zagreb, Zagreb, Croatia.
  • Chowdary P; Haemophilia Centre, University of Zagreb School of Medicine, Zagreb, Croatia.
  • Coppens M; Katharine Dormandy Haemophilia and Thrombosis Centre, Royal Free Hospital, London, UK.
  • Crato M; Department of Vascular Medicine, Hemophilia Treatment Center, Amsterdam UMC Location University of Amsterdam, Amsterdam, Netherlands.
  • Jimenez-Yuste V; Amsterdam Cardiovascular Sciences, Pulmonary Hypertension & Thrombosis, Amsterdam, The Netherlands.
  • Klamroth R; European Haemopilia Consortium, Brussels, Belgium.
  • Makris M; Hematology Department, Hospital Universitario La Paz-IdiPaz, Autonoma University, Madrid, Spain.
  • Mulders G; Department for Internal Medicine and Vascular Medicine, Haemophilia Treatment Center, Vivantes Hospital im Friedrichshain, Berlin, Germany.
  • Peyvandi F; Department of Infection, Immunity and Cardiovascular Disease, University of Sheffield, Sheffield, UK.
Haemophilia ; 30(3): 852-854, 2024 May.
Article em En | MEDLINE | ID: mdl-38462796

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Terapia Genética / Hemofilia A Limite: Humans Idioma: En Revista: Haemophilia Ano de publicação: 2024 Tipo de documento: Article

Texto completo: 1 Coleções: 01-internacional Base de dados: MEDLINE Assunto principal: Terapia Genética / Hemofilia A Limite: Humans Idioma: En Revista: Haemophilia Ano de publicação: 2024 Tipo de documento: Article