Detalhe da pesquisa
1.
Induction of fetal hemoglobin synthesis by CRISPR/Cas9-mediated editing of the human ß-globin locus.
Blood
; 131(17): 1960-1973, 2018 04 26.
Artigo
em Inglês
| MEDLINE | ID: mdl-29519807
2.
Optimization of CRISPR/Cas9 Delivery to Human Hematopoietic Stem and Progenitor Cells for Therapeutic Genomic Rearrangements.
Mol Ther
; 27(1): 137-150, 2019 01 02.
Artigo
em Inglês
| MEDLINE | ID: mdl-30424953
3.
Gene Therapy for ß-Hemoglobinopathies.
Mol Ther
; 25(5): 1142-1154, 2017 05 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-28377044
4.
Molecular and functional characterization of CD133+ stem/progenitor cells infused in patients with end-stage liver disease reveals their interplay with stromal liver cells.
Cytotherapy
; 19(12): 1447-1461, 2017 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-28917627
5.
GATA Factor-Mediated Gene Regulation in Human Erythropoiesis.
iScience
; 23(4): 101018, 2020 Apr 24.
Artigo
em Inglês
| MEDLINE | ID: mdl-32283524
6.
An Optimized Lentiviral Vector Efficiently Corrects the Human Sickle Cell Disease Phenotype.
Mol Ther Methods Clin Dev
; 10: 268-280, 2018 Sep 21.
Artigo
em Inglês
| MEDLINE | ID: mdl-30140714
7.
Concise Review: Epigenetic Regulation of Hematopoiesis: Biological Insights and Therapeutic Applications.
Stem Cells Transl Med
; 6(12): 2106-2114, 2017 12.
Artigo
em Inglês
| MEDLINE | ID: mdl-29080249