Detalhe da pesquisa
1.
CRISPR-targeted MAGT1 insertion restores XMEN patient hematopoietic stem cells and lymphocytes.
Blood
; 138(26): 2768-2780, 2021 12 30.
Artigo
em Inglês
| MEDLINE | ID: mdl-34086870
2.
Enhanced homology-directed repair for highly efficient gene editing in hematopoietic stem/progenitor cells.
Blood
; 137(19): 2598-2608, 2021 05 13.
Artigo
em Inglês
| MEDLINE | ID: mdl-33623984
3.
Correction of X-CGD patient HSPCs by targeted CYBB cDNA insertion using CRISPR/Cas9 with 53BP1 inhibition for enhanced homology-directed repair.
Gene Ther
; 28(6): 373-390, 2021 06.
Artigo
em Inglês
| MEDLINE | ID: mdl-33712802
4.
MAGT1 messenger RNA-corrected autologous T and natural killer cells for potential cell therapy in X-linked immunodeficiency with magnesium defect, Epstein-Barr virus infection and neoplasia disease.
Cytotherapy
; 23(3): 203-210, 2021 03.
Artigo
em Inglês
| MEDLINE | ID: mdl-33051095
5.
Differential impact of glucose levels and advanced glycation end-products on tubular cell viability and pro-inflammatory/profibrotic functions.
Biochem Biophys Res Commun
; 451(4): 627-31, 2014 Sep 05.
Artigo
em Inglês
| MEDLINE | ID: mdl-25130465
6.
Self-organized yolk sac-like organoids allow for scalable generation of multipotent hematopoietic progenitor cells from induced pluripotent stem cells.
Cell Rep Methods
; 3(4): 100460, 2023 04 24.
Artigo
em Inglês
| MEDLINE | ID: mdl-37159663
7.
Lentivector cryptic splicing mediates increase in CD34+ clones expressing truncated HMGA2 in human X-linked severe combined immunodeficiency.
Nat Commun
; 13(1): 3710, 2022 06 28.
Artigo
em Inglês
| MEDLINE | ID: mdl-35764638
8.
CRISPR-Cas9-AAV versus lentivector transduction for genome modification of X-linked severe combined immunodeficiency hematopoietic stem cells.
Front Immunol
; 13: 1067417, 2022.
Artigo
em Inglês
| MEDLINE | ID: mdl-36685559
9.
Spatial and temporal expression of CCR3 and the common beta chain of the IL-3, IL-5 and GM-CSF receptor in the nasal epithelium and lymphoid tissues in a rat model of allergic rhinitis.
Cytokine
; 52(3): 194-202, 2010 Dec.
Artigo
em Inglês
| MEDLINE | ID: mdl-20696593
10.
NOX4 is the main NADPH oxidase involved in the early stages of hematopoietic differentiation from human induced pluripotent stem cells.
Free Radic Biol Med
; 146: 107-118, 2020 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-31626946
11.
NADPH oxidase correction by mRNA transfection of apheresis granulocytes in chronic granulomatous disease.
Blood Adv
; 4(23): 5976-5987, 2020 12 08.
Artigo
em Inglês
| MEDLINE | ID: mdl-33284949
12.
CRISPR/Cas9 applications in gene therapy for primary immunodeficiency diseases.
Emerg Top Life Sci
; 3(3): 277-287, 2019 May 31.
Artigo
em Inglês
| MEDLINE | ID: mdl-33523134
13.
Ex Vivo Models of Chronic Granulomatous Disease.
Methods Mol Biol
; 1982: 587-622, 2019.
Artigo
em Inglês
| MEDLINE | ID: mdl-31172497
14.
Tumor microenvironment and clonal monocytes from chronic myelomonocytic leukemia induce a procoagulant climate.
Blood Adv
; 3(12): 1868-1880, 2019 06 25.
Artigo
em Inglês
| MEDLINE | ID: mdl-31221660
15.
Therapeutic effects of proteoliposomes on X-linked chronic granulomatous disease: proof of concept using macrophages differentiated from patient-specific induced pluripotent stem cells.
Int J Nanomedicine
; 12: 2161-2177, 2017.
Artigo
em Inglês
| MEDLINE | ID: mdl-28356734
16.
Genetic disorders coupled to ROS deficiency.
Redox Biol
; 6: 135-156, 2015 Dec.
Artigo
em Inglês
| MEDLINE | ID: mdl-26210446
17.
Optimized Generation of Functional Neutrophils and Macrophages from Patient-Specific Induced Pluripotent Stem Cells: Ex Vivo Models of X(0)-Linked, AR22(0)- and AR47(0)- Chronic Granulomatous Diseases.
Biores Open Access
; 3(6): 311-26, 2014 Dec 01.
Artigo
em Inglês
| MEDLINE | ID: mdl-25469316